日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Verdiperstat in Amyotrophic Lateral Sclerosis: Results From the Randomized HEALEY ALS Platform Trial

Verdiperstat治疗肌萎缩侧索硬化症:来自随机HEALEY ALS平台试验的结果

Andrews, Jinsy; Paganoni, Sabrina; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Young, Eufrosina; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Connolly, Mariah R; Berry, James D; D'Agostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Heitzman, Daragh; Ajroud-Driss, Senda; Appel, Stanley H; Shroff, Sheetal; Katz, Jonathan; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Goutman, Stephen A; Olney, Nicholas; Miller, Timothy; Fernandes, Joseph Americo; Ilieva, Hristelina; Jawdat, Omar; Weiss, Michael D; Foster, Laura; Vu, Tuan; Ladha, Shafeeq; Owegi, Margaret Ayo; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Swenson, Andrea; Heiman-Patterson, Terry; Caress, James; Fee, Dominic; Peltier, Amanda; Lewis, Richard; Rosenfeld, Jeffrey; Walk, David; Johnson, Kristin; Elliott, Matthew; Kasarskis, Edward J; Rutkove, Seward; McIlduff, Courtney E; Bedlack, Richard; Elman, Lauren; Goyal, Namita A; Rezania, Kourosh; Twydell, Paul; Benatar, Michael; Glass, Jonathan; Cohen, Jeffrey A; Jones, Vovanti; Zilliox, Lindsay; Wymer, James P; Beydoun, Said R; Shah, Jaimin; Pattee, Gary L; Martinez-Thompson, Jennifer; Nayar, Shakti; Granit, Volkan; Donohue, Mary; Grossman, Katheryn; Campbell, Daniel J; Qureshi, Irfan A; Cudkowicz, Merit E; Babu, Suma

Oligo-PROTAC strategy for cell-selective and targeted degradation of activated STAT3

Oligo-PROTAC 策略用于细胞选择性和靶向降解活化的 STAT3

Jeremy Hall, Zhuoran Zhang, Supriyo Bhattacharya, Dongfang Wang, Marice Alcantara, Yong Liang, Piotr Swiderski, Stephen Forman, Larry Kwak, Nagarajan Vaidehi, Marcin Kortylewski

Bi-functional CpG-STAT3 decoy oligonucleotide triggers multilineage differentiation of acute myeloid leukemia in mice

双功能 CpG-STAT3 诱饵寡核苷酸引发小鼠急性髓系白血病的多谱系分化

Dongfang Wang, Damian Kaniowski, Karol Jacek, Yu-Lin Su, Chunsong Yu, Jeremy Hall, Haiqing Li, Mingye Feng, Susanta Hui, Bożena Kaminska, Vittorio DeFranciscis, Carla Lucia Esposito, Annalisa DiRuscio, Bin Zhang, Guido Marcucci, Ya-Huei Kuo, Marcin Kortylewski

Targeting STAT3 in tumor-associated antigen-presenting cells as a strategy for kidney and bladder cancer immunotherapy

以肿瘤相关抗原呈递细胞中的STAT3为靶点,作为肾癌和膀胱癌免疫治疗的策略

Marice B Alcantara,Wilson S Tang,Dongfang Wang,Damian Kaniowski,Elaine Kang,Nazli Dizman ,Alexander Chehrazi-Raffle,Luis Meza,Zeynep Zengin,Jeremy Hall,JoAnn Hsu,Colt Egelston,Dayson Moreira,Alan Horsager,Sumanta K Pal,Marcin Kortylewski

Psychosis Endophenotypes: A Gene-Set-Specific Polygenic Risk Score Analysis

精神病内表型:基因集特异性多基因风险评分分析

Wang, Baihan; Irizar, Haritz; Thygesen, Johan H; Zartaloudi, Eirini; Austin-Zimmerman, Isabelle; Bhat, Anjali; Harju-Seppänen, Jasmine; Pain, Oliver; Bass, Nick; Gkofa, Vasiliki; Alizadeh, Behrooz Z; van Amelsvoort, Therese; Arranz, Maria J; Bender, Stephan; Cahn, Wiepke; Stella Calafato, Maria; Crespo-Facorro, Benedicto; Di Forti, Marta; Giegling, Ina; de Haan, Lieuwe; Hall, Jeremy; Hall, Mei-Hua; van Haren, Neeltje; Iyegbe, Conrad; Kahn, René S; Kravariti, Eugenia; Lawrie, Stephen M; Lin, Kuang; Luykx, Jurjen J; Mata, Ignacio; McDonald, Colm; McIntosh, Andrew M; Murray, Robin M; Picchioni, Marco; Powell, John; Prata, Diana P; Rujescu, Dan; Rutten, Bart P F; Shaikh, Madiha; Simons, Claudia J P; Toulopoulou, Timothea; Weisbrod, Matthias; van Winkel, Ruud; Kuchenbaecker, Karoline; McQuillin, Andrew; Bramon, Elvira

A high ratio of linoleic acid (n-6 PUFA) to alpha-linolenic acid (n-3 PUFA) adversely affects early stage of human neuronal differentiation and electrophysiological activity of glutamatergic neurons in vitro

亚油酸 (n-6 PUFA) 与 α-亚麻酸 (n-3 PUFA) 的比例过高会对人类神经元分化的早期阶段和谷氨酸能神经元的体外电生理活动产生不利影响

Karolina Dec, Mouhamed Alsaqati, Joanne Morgan, Sumukh Deshpande, Jamie Wood, Jeremy Hall, Adrian J Harwood

NRSF/REST lies at the intersection between epigenetic regulation, miRNA-mediated gene control and neurodevelopmental pathways associated with Intellectual disability (ID) and Schizophrenia

NRSF/REST 位于表观遗传调控、miRNA 介导的基因控制和与智力障碍 (ID) 和精神分裂症相关的神经发育通路的交叉点

Mouhamed Alsaqati, Brittany A Davis, Jamie Wood, Megan M Jones, Lora Jones, Aishah Westwood, Olena Petter, Anthony R Isles, David Linden, Marianne Van den Bree, Michael Owen, Jeremy Hall, Adrian J Harwood

Operationalizing a patient engagement plan for health research: Sharing a codesigned planning template from a national clinical trial

将患者参与健康研究计划付诸实施:分享来自一项国家临床试验的共同设计规划模板

Etchegary, Holly; Pike, Andrea; Patey, Andrea M; Gionet, Erin; Johnston, Brian; Goold, Susan; Francis, Vanessa; Grimshaw, Jeremy; Hall, Amanda

Developmental disruption to the cortical transcriptome and synaptosome in a model of SETD1A loss-of-function

SETD1A 功能丧失模型中皮质转录组和突触体的发育中断

Nicholas E Clifton, Matthew L Bosworth, Niels Haan, Elliott Rees, Peter A Holmans, Lawrence S Wilkinson, Anthony R Isles, Mark O Collins, Jeremy Hall