日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Harnessing whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluation

利用全人肝脏离体常温灌注进行临床前 AAV 载体评估

Marti Cabanes-Creus, Sophia H Y Liao, Renina Gale Navarro, Maddison Knight, Deborah Nazareth, Ngee-Soon Lau, Mark Ly, Erhua Zhu, Ramon Roca-Pinilla, Ricardo Bugallo Delgado, Ana F Vicente, Grober Baltazar, Adrian Westhaus, Jessica Merjane, Michael Crawford, Geoffrey W McCaughan, Carmen Unzu, Gloria

Development of CNS tropic AAV1-like variants with reduced liver-targeting following systemic administration in mice

在小鼠体内系统给药后,中枢神经系统嗜性 AAV1 样变体的产生及其肝脏靶向性的降低

Matthieu Drouyer, Jessica Merjane, Deborah Nazareth, Maddison Knight, Suzanne Scott, Sophia H Y Liao, Samantha L Ginn, Erhua Zhu, Ian E Alexander, Leszek Lisowski

Enhanced AAV transduction across preclinical CNS models: A comparative study in human brain organoids with cross-species evaluations

增强 AAV 在临床前 CNS 模型中的转导:对人类脑类器官进行跨物种评估的比较研究

Matthieu Drouyer, Jessica Merjane, Teodora Nedelkoska, Adrian Westhaus, Suzanne Scott, Scott Lee, Peter G R Burke, Simon McMullan, Jose L Lanciego, Ana F Vicente, Ricardo Bugallo, Carmen Unzu, Gloria González-Aseguinolaza, Anai Gonzalez-Cordero, Leszek Lisowski

CUTS RNA Biosensor for the Real-Time Detection of TDP-43 Loss-of-Function

CUTS RNA 生物传感器用于实时检测 TDP-43 功能丧失

Longxin Xie, Jessica Merjane, Cristian A Bergmann, Jiazhen Xu, Bryan Hurtle, Christopher J Donnelly

Novel AAV variants with improved tropism for human Schwann cells

对人类施万细胞具有更好趋向性的新型 AAV 变体

Matthieu Drouyer, Tak-Ho Chu, Elodie Labit, Florencia Haase, Renina Gale Navarro, Deborah Nazareth, Nicole Rosin, Jessica Merjane, Suzanne Scott, Marti Cabanes-Creus, Adrian Westhaus, Erhua Zhu, Rajiv Midha, Ian E Alexander, Jeff Biernaskie, Samantha L Ginn, Leszek Lisowski

Interferon inhibits the release of herpes simplex virus-1 from the axons of sensory neurons

干扰素抑制感觉神经元轴突释放单纯疱疹病毒-1

Kevin Danastas, Gerry Guo, Jessica Merjane, Nathan Hong, Ava Larsen, Monica Miranda-Saksena, Anthony L Cunningham