Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
Elexacaftor-Tezacaftor-Ivacaftor 用于治疗携带单个 Phe508del 等位基因的囊性纤维化
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa1908639
Middleton, Peter G; Mall, Marcus A; Dřevínek, Pavel; Lands, Larry C; McKone, Edward F; Polineni, Deepika; Ramsey, Bonnie W; Taylor-Cousar, Jennifer L; Tullis, Elizabeth; Vermeulen, François; Marigowda, Gautham; McKee, Charlotte M; Moskowitz, Samuel M; Nair, Nitin; Savage, Jessica; Simard, Christopher; Tian, Simon; Waltz, David; Xuan, Fengjuan; Rowe, Steven M; Jain, Raksha