Self-degradable "gemini-like" ionizable lipid-mediated delivery of siRNA for subcellular-specific gene therapy of hepatic diseases.
用于肝脏疾病亚细胞特异性基因治疗的自降解“双子型”可电离脂质介导的siRNA递送
期刊:Acta Pharmaceutica Sinica B
影响因子:14.6
doi:10.1016/j.apsb.2025.04.003
Wang Qiu, Wan Bin, Feng Yao, Yang Zimeng, Li Dan, Liu Fan, Gao Ya, Li Chang, Liu Yanhua, Sun Yongbing, He Zhonggui, Luo Cong, Sun Jin, Jiang Qikun