Dose-dependent effects of enzyme replacement therapy on skeletal disease progression in mucopolysaccharidosis VII dogs
酶替代疗法对粘多糖贮积症VII型犬骨骼疾病进展的剂量依赖性影响
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2022.11.006
Gawri, Rahul; Lau, Yian Khai; Lin, Gloria; Shetye, Snehal S; Zhang, Chenghao; Jiang, Zhirui; Abdoun, Khaled; Scanzello, Carla R; Jo, Stephanie Y; Mai, Wilfried; Dodge, George R; Casal, Margret L; Smith, Lachlan J