Comparative analysis of RNA versus protein splicing in dual AAV-mediated gene therapy in a mouse model of DFNB9 deafness.
在 DFNB9 耳聋小鼠模型中，对双重 AAV 介导的基因治疗中 RNA 与蛋白质剪接进行比较分析。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.10.002
Xun Mengzhao, Fan Xintai, Wang Hui, Zhao Jingjing, Tang Gongrui, Zhang Weida, Hu Shaowei, Zhang Longlong, Wang Daqi, Chen Yuxin, Liu Jianping, Tang Honghai, Li Geng-Lin, Chen Bing, Shu Yilai
