Experiences from treating seven adult 5q spinal muscular atrophy patients with Nusinersen
使用诺西那生治疗七名成年5q脊髓性肌萎缩症患者的经验
期刊:Therapeutic Advances in Neurological Disorders
影响因子:4.1
doi:10.1177/1756286420907803
Jochmann, Elisabeth; Steinbach, Robert; Jochmann, Thomas; Chung, Ha-Yeun; Rödiger, Annekathrin; Neumann, Rotraud; Mayer, Thomas E; Kirchhof, Klaus; Loudovici-Krug, Dana; Smolenski, Ulrich C; Witte, Otto W; Grosskreutz, Julian