日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CSF and blood neuronal injury biomarkers in spinal bulbar muscular atrophy and amyotrophic lateral sclerosis 4

脊髓延髓肌萎缩症和肌萎缩侧索硬化症4中脑脊液和血液神经元损伤生物标志物

Shahim, Pashtun; AlQahtani, Abdullah; Kokkinis, Angela D; Kazmi, Narjis; Ezuma-Ngwu, Marie; Misra, Jahan; Harmison, George; Benoit, Nicole; Jones, Melina; Howe, Elizabeth; Schindler, Alice B; Joe, Galen O; Grunseich, Christopher

Efficacy of Pomalidomide on Motor Performance and Functional Abilities in Patients with Steroid Refractory Chronic Graft Versus Host Disease: A Randomized Clinical Study

泊马度胺对类固醇难治性慢性移植物抗宿主病患者运动功能和功能能力的影响:一项随机临床研究

Jorgensen, Jessica J; Joe, Galen O; Jiménez-Silva, Rafael; Ho, Pei-Shu; Dunigan, Tiara; Mitchell, Sandra A; Pavletic, Steven Z; Curtis, Lauren M; Comis, Leora E

Identifying Clinical Measures Related to Falls in Ambulatory Patients with Spinal and Bulbar Muscular Atrophy

识别与脊髓延髓肌萎缩症可活动患者跌倒相关的临床指标

Shrader, Joseph A; Niemic, Allison C; Jiménez-Silva, Rafael; Woolstenhulme, Joshua G; Joe, Galen O; Jacobs, Uma; Sansare, Ashwini; Kokkinis, Angela; Fischbeck, Kenneth; Grunseich, Chris; Zampieri, Cris

Evaluation of Sensory and Motor Function in Spinal and Bulbar Muscular Atrophy Using Quiet Stance and Reactive Postural Control

利用安静站姿和反应性姿势控制评估脊髓延髓肌萎缩症患者的感觉和运动功能

Shrader, Joseph A; Sansare, Ashwini; Niemic, Allison C; Jiménez-Silva, Rafael; Woolstenhulme, Joshua G; Joe, Galen O; Jacobs, Uma; Kokkinis, Angela; Fischbeck, Kenneth; Grunseich, Chris; Zampieri, Cris

Metabolic syndrome prevalence and impact on outcomes in patients with chronic graft-versus-host disease

代谢综合征的患病率及其对慢性移植物抗宿主病患者预后的影响

Zhao, Aaron T; Pirsl, Filip; Steinberg, Seth M; Holtzman, Noa G; Schulz, Eduard; Mina, Alain; Mays, Jacqueline W; Cowen, Edward W; Comis, Leora E; Joe, Galen O; Yanovski, Jack A; Pavletic, Steven Z

Predictors and significance of kidney dysfunction in patients with chronic graft-versus-host disease

慢性移植物抗宿主病患者肾功能障碍的预测因素及其意义

Beshensky, David; Pirsl, Filip; Holtzman, Noa G; Steinberg, Seth M; Mays, Jacqueline W; Cowen, Edward W; Comis, Leora E; Joe, Galen O; Magone, M Teresa; Schulz, Eduard; Waldman, Meryl A; Pavletic, Steven Z

Determinants and Clinical Significance of Musculoskeletal Symptoms in Patients With Chronic Graft-Versus-Host Disease

慢性移植物抗宿主病患者肌肉骨骼症状的决定因素和临床意义

Zelic Kerep, Ana; Pirsl, Filip; Steinberg, Seth; Mitchell, Sandra; Curtis, Lauren; Holtzman, Noa; Goklemez, Sencer; Bilic, Ervina; Cowen, Edward; Pichard, Dominique; Joe, Galen; Comis, Leora; Im, Annie; Berger, Ann; Parsons-Wandell, Laura; Pulanic, Drazen; Baird, Kristin; Gress, Ronald; Pavletic, Steven

SAFETY AND TOLERABILITY OF STRENGTH TRAINING IN SPINAL AND BULBAR MUSCULAR ATROPHY: A CASE REPORT

脊髓延髓肌萎缩症患者力量训练的安全性和耐受性:病例报告

Shieh, Vincent; Zampieri, Cris; Stout, Paul; Joe, Galen O; Kokkinis, Angela; Fischbeck, Kenneth H; Grunseich, Christopher; Shrader, Joseph A

Skeletal Muscle Magnetic Resonance Biomarkers in GNE Myopathy

GNE肌病中的骨骼肌磁共振生物标志物

Liu, Chia-Ying; Yao, Jianhua; Kovacs, William C; Shrader, Joseph A; Joe, Galen; Ouwerkerk, Ronald; Mankodi, Ami K; Gahl, William A; Summers, Ronald M; Carrillo, Nuria

Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study

N-乙酰甘露糖胺 (ManNAc) 治疗 GNE 肌病患者的安全性和有效性:一项开放标签的 II 期研究

Carrillo, Nuria; Malicdan, May C; Leoyklang, Petcharat; Shrader, Joseph A; Joe, Galen; Slota, Christina; Perreault, John; Heiss, John D; Class, Bradley; Liu, Chia-Ying; Bradley, Kennan; Jodarski, Colleen; Ciccone, Carla; Driscoll, Claire; Parks, Rebecca; Van Wart, Scott; Bayman, Levent; Coffey, Christopher S; Quintana, Melanie; Berry, Scott M; Huizing, Marjan; Gahl, William A