Ex vivo Improvement of a von Willebrand Disease Type 2A Phenotype Using an Allele-Specific Small-Interfering RNA
使用等位基因特异性小干扰 RNA 体外改善 2A 型血管性血友病表型
期刊:Thrombosis and Haemostasis
影响因子:5
doi:10.1055/s-0040-1715442
Annika de Jong, Richard J Dirven, Johan Boender, Ferdows Atiq, Seyed Yahya Anvar, Frank W G Leebeek, Bart J M van Vlijmen, Jeroen Eikenboom