Highly conserved brain vascular receptor ALPL mediates transport of engineered AAV vectors across the blood-brain barrier.
高度保守的脑血管受体ALPL介导工程化AAV载体跨越血脑屏障的运输。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.04.046
Moyer Tyler C, Hoffman Brett A, Chen Weitong, Shah Ishan, Ren Xiao-Qin, Knox Tatiana, Liu Jiachen, Wang Wei, Li Jiangyu, Khalid Hamza, Kulkarni Anupriya S, Egbuchulam Munachiso, Clement Joseph, Bloedel Alexis, Child Matthew, Kaur Rupinderjit, Rouse Emily, Graham Kristin, Maura Damien, Thorpe Zachary, Sayed-Zahid Ambreen, Hiu-Yan Chung Charlotte, Kutchin Alexander, Johnson Amy, Yao Johnny, Thompson Jeffrey, Pande Nilesh, Nonnenmacher Mathieu E