Drug screen in iPSC-Neurons identifies nucleoside analogs as inhibitors of (G4C2)n expression in C9orf72 ALS/FTD
iPSC-Neurons 中的药物筛选鉴定出核苷类似物是 C9orf72 ALS/FTD 中 (G4C2)n 表达的抑制剂
期刊:Cell Reports
影响因子:7.5
doi:10.1016/j.celrep.2022.110913
Mareike Czuppa, Ashutosh Dhingra, Qihui Zhou, Carina Schludi, Laura König, Elisabeth Scharf, Daniel Farny, Anupriya Dalmia, Joachim Täger, Melissa Castillo-Lizardo, Eszter Katona, Kohji Mori, Tina Aumer, Florian Schelter, Markus Müller, Thomas Carell, Tuomo Kalliokoski, Josef Messinger, Patrizia Riz