Inhibition of Glycogen Synthase II with RNAi Prevents Liver Injury in Mouse Models of Glycogen Storage Diseases
利用 RNAi 抑制糖原合酶 II 可预防糖原累积症小鼠模型中的肝损伤
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2018.04.023
Natalie Pursell, Jessica Gierut, Wei Zhou, Michael Dills, Rohan Diwanji, Monika Gjorgjieva, Utsav Saxena, Jr-Shiuan Yang, Anee Shah, Nandini Venkat, Rachel Storr, Boyoung Kim, Weimin Wang, Marc Abrams, Margaux Raffin, Gilles Mithieux, Fabienne Rajas, Henryk Dudek, Bob D Brown, Chengjung Lai