日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Monitoring biological effects of somatic cell genome editing

监测体细胞基因组编辑的生物学效应

Freedman, Benjamin S; Bulte, Jeff W M; Conklin, Bruce R; Judge, Luke M; Dwinell, Melinda R; Geurts, Aron M; Sitton, Madeleine J; Mahajan, Vineet; Kiani, Samira; Gersbach, Charles A; Ebrahimkhani, Mo R; Kelly, John J; Ronald, John A; Morizane, Ryuji; Gupta, Navin; Shakeri-Zadeh, Ali; Vo, Nicole; Saha, Krishanu; Saxena, Shivani; Gamm, David M; Sinha, Divya; Tarantal, Alice F; Vandsburger, Moriel; Matsubara, Azusa; Fu, Hongxia; Tsai, Shengdar Q

RBM20 Truncating Variants and Human Cardiomyopathy

RBM20截断变异体与人类心肌病

Floyd, Brendan J; Njoroge, Joyce N; Krysov, Vikki A; Gomes, Bruna; Murtha, Ryan; Aribeana, Chiaka; Cannie, Douglas; Smith, Eric; Paldino, Alessia; Brown, Emily E; Barth, Andreas; Ilhan, Erkan; Johnson, Renee; Wojciak, Julianne; Alkhayat, Mohamad; Graw, Sharon; Medo, Kristen; Haas, Jan; Chahal, C Anwar A; Fenzl, Kai; Steinmetz, Lars; Gollob, Michael; Ashley, Euan; Day, Sharlene; Judge, Daniel; Roberts, Jason D; Vedantham, Vasanth; Mao, Chad Y; Fatkin, Diane; Lakdawala, Neal K; Taylor, Matthew R G; Mestroni, Luisa; Saguner, Ardan M; Tayal, Upasana; Cadrin-Tourigny, Julia; Krahn, Andrew D; James, Cynthia; Dal Ferro, Matteo; Sinagra, Gianfranco; Merlo, Marco; Owens, Anjali; Reza, Nosheen; Saberi, Sara; Helms, Adam; Elliott, Perry; Meder, Benjamin; Lancaster, Megan; Parikh, Victoria N

Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension

Acoramidis治疗野生型和变异型转甲状腺素蛋白淀粉样变性心肌病的疗效:来自ATTRibute-CM及其开放标签扩展研究的结果

Alexander, Kevin M; Davis, Margot K; Akinboboye, Olakunle; Berk, John; Bhatt, Kunal; Cappelli, Francesco; Cuddy, Sarah A M; Fontana, Marianna; Garcia-Pavia, Pablo; Gillmore, Julian D; Griffin, Jan M; Grodin, Justin L; Judge, Daniel P; Khouri, Michel G; Lam, Kaitlyn; Masri, Ahmad; Maurer, Mathew S; Obici, Laura; Ruberg, Frederick L; Sarswat, Nitasha; Shah, Keyur; Soman, Prem; Stern, Lily; Wright, Richard; Xiong, Kuangnan; Cao, Xiaofan; Lystig, Ted; Tamby, Jean-François; Castaño, Adam; Katz, Leonid; Sinha, Uma; Fox, Jonathan C; Solomon, Scott D; Grogan, Martha

Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial

Acoramidis治疗转甲状腺素蛋白淀粉样变性心肌病的长期疗效:ATTRibute-CM随机临床试验的开放标签扩展研究

Soman, Prem; Cuddy, Sarah A M; Gillmore, Julian D; Sarswat, Nitasha; Judge, Daniel P; Cappelli, Francesco; Stern, Lily K; Wright, Richard; Akinboboye, Olakunle; Obici, Laura; Bhatt, Kunal; Xiong, Kuangnan; Castaño, Adam; Chen, Chris; Falvey, Heather; Pecoraro, Maria Lucia; Tamby, Jean-François; Sinha, Uma; Fox, Jonathan C; Shah, Keyur; Grodin, Justin L; Ambardekar, Amrut V; Alexander, Kevin M; Khouri, Michel G; Cheng, Richard K

Haplotype editing with CRISPR-Cas9 as a therapeutic approach for dominant-negative missense mutations in NEFL

利用 CRISPR-Cas9 进行单倍型编辑作为治疗 NEFL 中显性负性错义突变的治疗方法

Dua, Poorvi H; Simon, Bazilco M J; Marley, Chiara B E; Feliciano, Carissa M; Watry, Hannah L; Cowan, Quinn T; Steury, Dylan; Abraham, Abin; Gilbertson, Erin N; Ramey, Grace D; Capra, John A; Conklin, Bruce R; Judge, Luke M

Clinical Decision Support for Antibiotic Prescribing Duration in Children With Acute Otitis Media

儿童急性中耳炎抗生素处方疗程的临床决策支持

Mason, Matt; Slovin, Sara Ruth; Zomorrodi, Arezoo; Chan, Shannon; Judge, Rebecca; Vodzak, Jennifer; Shapiro, Craig

Peptide concentration gradients and aligned microfiber topography synergize to speed and direct Schwann cell migration

肽浓度梯度和排列有序的微纤维形貌协同作用,加速并引导雪旺细胞迁移

Chan, Yin Mei; Hu, Yang; Judge, Nicola G; Willits, Rebecca K; Becker, Matthew L

Why current risk factor-based approaches fall short in predicting stillbirth: a national cohort study of nulliparous women in England

为什么目前基于风险因素的方法在预测死产方面存在不足:一项针对英国初产妇的全国性队列研究

Howell, A; Thilaganathan, B; Margelyte, R; Burden, C; Cheng, V; Sandall, J; Viner, M; Brigante, L; Anumba, D; Winter, C; Harlev-Lam, B; Draycott, T; Judge, A; Lenguerrand, E

The Immune Biology of the Adrenal Gland Microenvironment and Its Role in Metastatic Progression

肾上腺微环境的免疫生物学及其在转移进展中的作用

Liu, Natalie M; Sholevar, Cyrus J; Karimzadeh, Makan; Uppuluri, Jay; Van Dongen, Clemens; Graves, Claire E; Campbell, Michael J; Zamora, Anthony E; Judge, Sean J; Canter, Robert J

Benzodiazepine Co-Exposure Among Patients Presenting to the Emergency Department With a Confirmed Opioid Overdose

急诊科收治的阿片类药物过量患者中苯二氮卓类药物合并暴露情况

Hughes, Adrienne; Spungen, Hannah; Culbreth, Rachel; Aldy, Kim; Krotulski, Alex; Hendrickson, Robert G; Amaducci, Alexandra; Judge, Bryan; Meaden, Christopher; Calello, Diane P; Buchanan, Jennie; Carpenter, Joseph; Shulman, Joshua; Brent, Jeffrey; Wax, Paul; Campleman, Sharan; Levine, Michael; Schwarz, Evan; Manini, Alex F