Biodistribution and Tolerability of AAV-PHP.B-CBh- SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles
AAV-PHP.B-CBh-SMN1 在 Wistar Han 大鼠和食蟹猴体内的生物分布和耐受性显示出不同的毒理学特征
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2021.116
Xavier Palazzi, Ingrid D Pardo, Madhu P Sirivelu, Leah Newman, Steven W Kumpf, Jessie Qian, Tania Franks, Sarah Lopes, June Liu, Laura Monarski, Sandra Casinghino, Casey Ritenour, Hayley Ritenour, Christopher Dubois, Jennifer Olson, John Graves, Kristin E Alexander, Timothy Coskran, Thomas A Lanz, J