日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Malignancy and gene therapy in hemophilia

恶性肿瘤和血友病基因治疗

期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.103283
Kaczmarek, Radoslaw
基因治疗
肿瘤
肿瘤免疫
发表日期：2026
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Hemophilia B gene therapy: a NAb-solute barrier overcome by adeno-associated virus serotype 5

B型血友病基因治疗：腺相关病毒5型血清型克服中和抗体屏障

期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2026.103428
Kaczmarek, Radoslaw
基因治疗
微生物学
发表日期：2026
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Current Status of Clinical Gene Therapy for Hemophilia and Globin Disorders

血友病和珠蛋白疾病临床基因治疗的现状

期刊:Journal of Blood Medicine
影响因子:2.7
doi:10.2147/JBM.S576017
Winkler, Rebecca; Herath, Ishan; Kaczmarek, Radoslaw; Xiao, Weidong; Herzog, Roland W; Severeid, Paige E
基因治疗
发表日期：2026
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Second gene therapy for hemophilia B approved: More answers or questions?

第二款用于治疗B型血友病的基因疗法获批：是更多答案还是更多疑问？

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.11.026
Kaczmarek, Radoslaw; Pierce, Glenn F
发表日期：2025
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Gene therapy for hemophilia - From basic science to first approvals of "one-and-done" therapies

血友病基因疗法——从基础科学到“一次性”疗法的首次获批

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.03.043
Herzog, Roland W; Kaczmarek, Radoslaw; High, Katherine A
发表日期：2025
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Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study

在etranacogene dezaparvovec 3期研究导入期，B型血友病成人患者体内已存在的AAV5抗体的自然史

期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101568
Klamroth, Robert; Recht, Michael; Key, Nigel S; Miesbach, Wolfgang; Pipe, Steven W; Kaczmarek, Radoslaw; Drelich, Douglass; Salazar, Blanca; Le Quellec, Sandra; Monahan, Paul E; Galante, Nicholas; van der Valk, Paul; Tarrant, Jacqueline
发表日期：2025
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Why is the uptake of gene therapy in hemophilia less than expected?

为什么血友病患者接受基因治疗的比例低于预期？

期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.102948
Pierce, Glenn F; Skinner, Mark; O'Mahony, Brian; Rotellini, Dawn; Kaczmarek, Radoslaw
基因治疗
发表日期：2025
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Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps

腺相关病毒介导的血友病基因治疗——弥补现有差距

期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2024.102673
Miesbach, Wolfgang; Batty, Paul; Chowdary, Pratima; Fong, Sylvia; Kaczmarek, Radoslaw; Leebeek, Frank W G; Long, Brian; Mahlangu, Johnny; Makris, Mike; Pierce, Glenn F; Pipe, Steven W; Srivastava, Alok; Voorberg, Jan; Peyvandi, Flora
微生物学
基因治疗
发表日期：2025
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Trends in Treatment of Severe Haemophilia and Impact on Inhibitor Assessment by the EUHASS Registry

EUHASS注册中心重型血友病治疗趋势及其对抑制剂评估的影响

期刊:Haemophilia
影响因子:3
doi:10.1111/hae.70039
Fischer, Kathelijn; Lassila, Riitta; Peyvandi, Flora; Gatt, Alex; Gouw, Samantha C; Hollingsworth, Rob; Lambert, Thierry; Kaczmarek, Radoslaw; Carbonero, Diana; Makris, Michael
发表日期：2025
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P1PK blood group antigens in birds: implications for veterinary blood transfusion, human and pet health

鸟类P1PK血型抗原：对兽医输血、人类和宠物健康的影响

期刊:BMC Veterinary Research
影响因子:2.6
doi:10.1186/s12917-025-05209-6
Bereznicka, Anna; Duk, Maria; Kapczynska, Katarzyna; Modlinska, Anna; Piasecki, Tomasz; Link-Lenczowski, Paweł; Heidorn-Czarna, Małgorzata; Pasikowski, Pawel; Czerwinski, Marcin; Kaczmarek, Radoslaw
发表日期：2025
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