A Quantitative Systems Pharmacology Model of Gaucher Disease Type 1 Provides Mechanistic Insight Into the Response to Substrate Reduction Therapy With Eliglustat
戈谢病1型定量系统药理学模型揭示了依利格鲁司他底物减少疗法的治疗机制。
期刊:Cpt-Pharmacometrics & Systems Pharmacology
影响因子:3
doi:10.1002/psp4.12506
Abrams, Ruth; Kaddi, Chanchala D; Tao, Mengdi; Leiser, Randolph J; Simoni, Giulia; Reali, Federico; Tolsma, John; Jasper, Paul; van Rijn, Zachary; Li, Jing; Niesner, Bradley; Barrett, Jeffrey S; Marchetti, Luca; Peterschmitt, M Judith; Azer, Karim; Neves-Zaph, Susana