日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Single-cell atlas of the aging mouse colon

衰老小鼠结肠的单细胞图谱

Dovydas Širvinskas ,Omid Omrani ,Jing Lu ,Mahdi Rasa ,Anna Krepelova ,Lisa Adam ,Sandra Kaeppel ,Felix Sommer ,Francesco Neri

In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

腺相关病毒载体宫内转移在猕猴模型中产生长期的 IX 因子水平

Citra N Z Mattar, Irene Gil-Farina, Cecilia Rosales, Nuryanti Johana, Yvonne Yi Wan Tan, Jenny McIntosh, Christine Kaeppel, Simon N Waddington, Arijit Biswas, Mahesh Choolani, Manfred Schmidt, Amit C Nathwani, Jerry K Y Chan

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients

重组AAV整合与非人灵长类动物和患者的肝脏遗传毒性无关

Gil-Farina, Irene; Fronza, Raffaele; Kaeppel, Christine; Lopez-Franco, Esperanza; Ferreira, Valerie; D'Avola, Delia; Benito, Alberto; Prieto, Jesus; Petry, Harald; Gonzalez-Aseguinolaza, Gloria; Schmidt, Manfred

Presence of a trs-Like Motif Promotes Rep-Mediated Wild-Type Adeno-Associated Virus Type 2 Integration

trs样基序的存在促进Rep介导的野生型腺相关病毒2型整合

Petri, Karl; Gabriel, Richard; Agundez, Leticia; Fronza, Raffaele; Afzal, Saira; Kaeppel, Christine; Linden, R Michael; Henckaerts, Els; Schmidt, Manfred

Integration frequency and intermolecular recombination of rAAV vectors in non-human primate skeletal muscle and liver

rAAV载体在非人灵长类动物骨骼肌和肝脏中的整合频率和分子间重组

Nowrouzi, Ali; Penaud-Budloo, Magalie; Kaeppel, Christine; Appelt, Uwe; Le Guiner, Caroline; Moullier, Philippe; von Kalle, Christof; Snyder, Richard O; Schmidt, Manfred

Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques

0.9G 自互补腺相关病毒载体 5 和 8 在恒河猴宫内进行基因转移后稳定表达人 FIX

Citra N Z Mattar, Amit C Nathwani, Simon N Waddington, Niraja Dighe, Christine Kaeppel, Ali Nowrouzi, Jenny Mcintosh, Nuryanti B Johana, Bryan Ogden, Nicholas M Fisk, Andrew M Davidoff, Anna David, Donald Peebles, Marcus B Valentine, Jens-Uwe Appelt, Christof von Kalle, Manfred Schmidt, Arijit Biswa

Complete genome sequence of Marinobacter adhaerens type strain (HP15), a diatom-interacting marine microorganism

海洋杆菌粘附型菌株(HP15)的完整基因组序列,该菌株是一种与硅藻相互作用的海洋微生物。

Gärdes, Astrid; Kaeppel, Eva; Shehzad, Aamir; Seebah, Shalin; Teeling, Hanno; Yarza, Pablo; Glöckner, Frank Oliver; Grossart, Hans-Peter; Ullrich, Matthias S