A small molecule that induces translational readthrough of CFTR nonsense mutations by eRF1 depletion
通过 eRF1 消耗来诱导 CFTR 无义突变翻译读通的小分子
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-021-24575-x
Jyoti Sharma #, Ming Du #, Eric Wong, Venkateshwar Mutyam, Yao Li, Jianguo Chen, Jamie Wangen, Kari Thrasher, Lianwu Fu, Ning Peng, Liping Tang, Kaimao Liu, Bini Mathew, Robert J Bostwick, Corinne E Augelli-Szafran, Hermann Bihler, Feng Liang, Jerome Mahiou, Josef Saltz, Andras Rab, Jeong Hong, Eric