日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

AAVrh.10 delivery of novel APOE2-Christchurch variant suppresses amyloid and Tau pathology in Alzheimer's disease mice.

AAVrh.10 递送新型 APOE2-Christchurch 变体可抑制阿尔茨海默病小鼠的淀粉样蛋白和 Tau 病理

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.11.003
Günaydin Caner, Sondhi Dolan, Kaminsky Stephen M, Lephart Hailey C, Leopold Philip L, Hackett Neil R, Khanna Richie, Crystal Ronald G
免疫/内分泌
发表日期：2024
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Twenty-Year Survival Analysis of Adeno-Associated Virus Vector Serotype 2-Mediated Gene Therapy to the Central Nervous System for CLN2 Disease

腺相关病毒载体2型介导的中枢神经系统基因治疗CLN2疾病的20年生存分析

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2024.182
Sondhi, Dolan; Kaminsky, Stephen M; Rosenberg, Jonathan B; Rostami, Mahboubeh R; Hackett, Neil R; Crystal, Ronald G
微生物学
基因治疗
神经科学
发表日期：2024
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Vectorized Human Antibody-Mediated Anti-Eosinophil Gene Therapy.

载体化人抗体介导的抗嗜酸性粒细胞基因治疗

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2024.165
Gioulvanidou Maria, Sarklioglu Selenay, Chen Xinlei, Lebedeva Irina V, Inalman Yeliz, Pohl Mary Ann, Bourne Lloyd, Andrew David, Lorenz Ivo C, Stiles Katie M, Pagovich Odelya E, Hackett Neil R, Kaminsky Stephen M, de Mulder Rougvie Miguel, Crystal Ronald G
细胞生物学
Human
细胞基因治疗
发表日期：2024
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Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

静脉注射编码抗氧化人α1-抗胰蛋白酶的AAV8载体治疗α1-抗胰蛋白酶缺乏症的安全性

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2022.192
Rosenberg, Jonathan B; De, Bishnu P; Greco, Alessandria; Gorman, Nicholas; Kooner, Vikrum; Chen, Alvin; Yost-Bido, Melissa; Munoz-Zuluaga, Carlos; Kaminsky, Stephen M; Rostami, Mahboubeh; Monette, Sébastien; Crystal, Ronald G; Sondhi, Dolan
Human
发表日期：2023
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Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia

确定治疗弗里德赖希共济失调心脏表现的安全有效静脉注射AAVrh.10hFXN剂量

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.020
Munoz-Zuluaga, Carlos; Gertz, Monica; Yost-Bido, Melissa; Greco, Alessandria; Gorman, Nicholas; Chen, Alvin; Kooner, Vikrum; Rosenberg, Jonathan B; De, Bishnu P; Kaminsky, Stephen M; Borczuk, Alain; Ricart Arbona, Rodolfo J; Martin, Heather R; Monette, Sebastien; Khanna, Richie; Barth, Jay A; Crystal, Ronald G; Sondhi, Dolan
发表日期：2023
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Assessment of Residual Full-Length SV40 Large T Antigen in Clinical-Grade Adeno-Associated Virus Vectors Produced in 293T Cells

对在 293T 细胞中生产的临床级腺相关病毒载体中残留的全长 SV40 大 T 抗原进行评估

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.032
De, Bishnu P; Cram, Sara; Lee, Hyunmi; Rosenberg, Jonathan B; Sondhi, Dolan; Crystal, Ronald G; Kaminsky, Stephen M
微生物学
细胞生物学
T细胞
发表日期：2023
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Positron Emission Tomography Quantitative Assessment of Off-Target Whole-Body Biodistribution of I-124-Labeled Adeno-Associated Virus Capsids Administered to Cerebral Spinal Fluid

正电子发射断层扫描定量评估经脑脊液给药的碘-124标记腺相关病毒衣壳的非靶向全身生物分布

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.060
Rosenberg, Jonathan B; Fung, Edward K; Dyke, Jonathan P; De, Bishnu P; Lou, Howard; Kelly, James M; Reejhsinghani, Layla; Ricart Arbona, Rodolfo J; Sondhi, Dolan; Kaminsky, Stephen M; Cartier, Nathalie; Hinderer, Christian; Hordeaux, Juliette; Wilson, James M; Ballon, Douglas J; Crystal, Ronald G
微生物学
神经科学
发表日期：2023
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Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease

在非人灵长类动物中，通过脑池内给药评估 AAVrh.10hCLN2 治疗 CLN2 巴顿病的安全性和生物分布

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.067
De, Bishnu P; Rosenberg, Jonathan B; Selvan, Nithya; Wilson, Isabelle; Yusufzai, Nadir; Greco, Alessandria; Kaminsky, Stephen M; Heier, Linda A; Ricart Arbona, Rodolfo J; Miranda, Ileana C; Monette, Sebastien; Nair, Anju; Khanna, Richie; Crystal, Ronald G; Sondhi, Dolan
Primate
神经科学
发表日期：2023
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Preclinical safety and biodistribution assessment of Ad-KCNH2-G628S administered via atrial painting in New Zealand white rabbits

通过心房涂染法在新西兰白兔中评估Ad-KCNH2-G628S的临床前安全性和生物分布

期刊:Basic & Clinical Pharmacology & Toxicology
影响因子:3.3
doi:10.1111/bcpt.13885
Benson, Janet M; Wang, Gensheng; Hutt, Julie A; Wu, Guodong; Kaminsky, Stephen M; Cram, Sara; Barur, Rajeshkumar; Donahue, J Kevin
KCNH2
发表日期：2023
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56326 Heart to Heart: An Interdisciplinary Community Collaboration to Address Health Disparities Through Cardiovascular Disease Risk Assessments in Underserved Urban Neighborhoods

56326 心连心：一项跨学科社区合作项目，旨在通过对服务不足的城市社区进行心血管疾病风险评估来解决健康差异问题

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2020.269
Rosenberg, Jonathan B; Chen, Alvin; De, Bishnu P; Dyke, Jonathan P; Ballon, Douglas J; Monette, Sebastien; Ricart Arbona, Rodolfo J; Kaminsky, Stephen M; Crystal, Ronald G; Sondhi, Dolan; Bang, Jakyung; Drozdz, Marek M; Dong, Lauren; Merghoub, Taha; Zippin, Jonathan H; Bales, Michael E; Zhu, Jifeng; Aboharb, Farid; Dusaj, Neville; Shtayer, Lior; Balaji, Venkatesh; Keeler, Allegra; Ganzer, Christine A; Ryon, Krista A; Ehrmann, Brett J; Imperato-McGinley, Julianne
心血管疾病
心血管
发表日期：2021
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