Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs
通过优化先导编辑和肺靶向脂质纳米颗粒,实现有效的囊性纤维化基因治疗
期刊:Frontiers in Systems Biology
影响因子:2.3
doi:10.3389/fsysb.2025.1603749
Lange, Kaya Sophie; Wiesner, Lisa Marie; Susat, Kathleen; Köhler, Vera; Lenger, Malte; Michalek, Christian Alexander; Baack, Anna-Lena; Mundt, Philip Frederic; Kanthak, Kai; Guckes, Isabell Alexandra; Sanfilippo, Liliana; Haverkamp, Lucas; Mahajan, Utkarsh Anil; Zimmer, Felicitas Helena; Zimmermann, Sinan; Radukic, Marco Tobias; Klages, Levin Joe; Kalinowski, Jörn; Müller, Kristian Mark