日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

FOP: From Biomolecules to Hope

FOP:从生物分子到希望

Kaplan, Frederick S; Pignolo, Robert J

Identifying global trends from case reports of fibrodysplasia ossificans progressiva: a scoping review

从进行性骨化性纤维发育不良病例报告中识别全球趋势:一项范围界定综述

Scott, Christiaan; Al Mukaddam, Mona; Davis, Michelle; De Cunto, Carmen L; Hsiao, Edward C; Pignolo, Robert J; Schwegler, Odette; Artyomenko, Alexander; Croskery, Kim; Hanman, Kate; Sanchot, Boris; Warnants, Emma; Kaplan, Frederick S

Ectopic pseudojoints in fibrodysplasia ossificans progressiva

进行性骨化性纤维发育不良中的异位假关节

Pignolo, Robert J; Al Mukaddam, Mona; Broski, Stephen; Morhart, Rolf; Drake, Luke T; Kneeland, Bruce; Towler, O Will; Kaplan, Frederick S

Medical guidelines for fibrodysplasia ossificans progressiva

进行性骨化性纤维发育不良症的医疗指南

Kaplan, Frederick S; Al Mukaddam, Mona; Baujat, Genevieve; Hidalgo Bravo, Alberto; Brown, Matthew; Cali, Amanda; Cho, Tae-Joon; Crowe, Corrie; De Cunto, Carmen L; Delai, Patricia L R; Diecidue, Robert J; Eekhoff, Elisabeth Marelise W; Friedlander, Lisa; Friedman, Clive S; Grunwald, Zvi; Haga, Nobuhiko; Hsiao, Edward C; Keen, Richard; Kitterman, Joseph A; Levy, Charles; Madhuri, Vrisha; Morhart, Rolf; Netelenbos, J Coen; Scott, Christiaan; Shore, Eileen M; Zasloff, Michael; Zhang, Keqin; Pignolo, Robert J

Characterization of flare-ups and impact of garetosmab in adults with fibrodysplasia ossificans progressiva: a post hoc analysis of the randomized, double-blind, placebo-controlled LUMINA-1 trial

对进行性骨化性纤维发育不良成人患者病情加重及garetosmab疗效的描述:一项随机、双盲、安慰剂对照LUMINA-1试验的事后分析

Keen, Richard; Dahir, Kathryn M; McGinniss, Jennifer; Sanchez, Robert J; Mellis, Scott; Economides, Aris N; Di Rocco, Maja; Orcel, Philippe; Roux, Christian; Tabarkiewicz, Jacek; Bachiller-Corral, Javier; Cheung, Angela M; Al Mukaddam, Mona; Mohammadi, Kusha; Gu, Jing; Srinivasan, Dushyanth; Trotter, Dinko Gonzalez; Eekhoff, E Marelise W; Kaplan, Frederick S; Pignolo, Robert J

Matrix metalloproteinase-9 deficiency confers resilience in fibrodysplasia ossificans progressiva in a man and mice.

基质金属蛋白酶-9 缺乏症可使人类和小鼠的进行性骨化性纤维发育不良症具有抵抗力

Lounev Vitali, Groppe Jay C, Brewer Niambi, Wentworth Kelly L, Smith Victoria, Xu Meiqi, Schomburg Lutz, Bhargava Pankaj, Al Mukaddam Mona, Hsiao Edward C, Shore Eileen M, Pignolo Robert J, Kaplan Frederick S

Cell Senescence in Heterotopic Ossification

异位骨化中的细胞衰老

Pignolo, Robert J; Kaplan, Frederick S; Wang, Haitao

Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trial

Garetosmab治疗进行性骨化性纤维发育不良:一项随机、双盲、安慰剂对照的II期试验

Di Rocco, Maja; Forleo-Neto, Eduardo; Pignolo, Robert J; Keen, Richard; Orcel, Philippe; Funck-Brentano, Thomas; Roux, Christian; Kolta, Sami; Madeo, Annalisa; Bubbear, Judith S; Tabarkiewicz, Jacek; Szczepanek, Małgorzata; Bachiller-Corral, Javier; Cheung, Angela M; Dahir, Kathryn M; Botman, Esmée; Raijmakers, Pieter G; Al Mukaddam, Mona; Tile, Lianne; Portal-Celhay, Cynthia; Sarkar, Neena; Hou, Peijie; Musser, Bret J; Boyapati, Anita; Mohammadi, Kusha; Mellis, Scott J; Rankin, Andrew J; Economides, Aris N; Trotter, Dinko Gonzalez; Herman, Gary A; O'Meara, Sarah J; DelGizzi, Richard; Weinreich, David M; Yancopoulos, George D; Eekhoff, E Marelise W; Kaplan, Frederick S

Polypeptide Substrate Accessibility Hypothesis: Gain-of-Function R206H Mutation Allosterically Affects Activin Receptor-like Protein Kinase Activity

多肽底物可及性假说:功能获得性R206H突变通过变构作用影响激活素受体样蛋白激酶活性

Groppe, Jay C; Lu, Guorong; Tandang-Silvas, Mary R; Pathi, Anupama; Konda, Shruti; Wu, Jingfeng; Le, Viet Q; Culbert, Andria L; Shore, Eileen M; Wharton, Kristi A; Kaplan, Frederick S

Most Fractures Treated Nonoperatively in Individuals With Fibrodysplasia Ossificans Progressiva Heal With a Paucity of Flareups, Heterotopic Ossification, and Loss of Mobility

大多数接受非手术治疗的进行性骨化性纤维发育不良患者的骨折愈合后,很少出现复发、异位骨化和活动受限的情况。

Lindborg, Carter M; Al Mukaddam, Mona; Baujat, Genevieve; Cho, Tae-Joon; De Cunto, Carmen L; Delai, Patricia L R; Eekhoff, Elisabeth M W; Haga, Nobuhiko; Hsiao, Edward C; Morhart, Rolf; de Ruiter, Ruben; Scott, Christiaan; Seemann, Petra; Szczepanek, Małgorzata; Tabarkiewicz, Jacek; Pignolo, Robert J; Kaplan, Frederick S