日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Contaminating plasmid sequences and disrupted vector genomes in the liver following adeno-associated virus gene therapy

腺相关病毒基因治疗后肝脏中存在的污染质粒序列和破坏的载体基因组

Buddle, Sarah; Brown, Li-An K; Morfopoulou, Sofia; Torres Montaguth, Oscar Enrique; Scoto, Mariacristina; Herder, Vanessa; Dhawan, Anil; Brown, Julianne R; Atkinson, Laura; Kopec, Angelika; Davis, Dee; Storey, Nathaniel; Campos, Luis; Sebire, Neil; Macpherson, Hannah; Lee, Jasmaine; Orton, Richard; Baranello, Giovanni; Asamaphan, Patawee; Ilia, Georgios; Karda, Rajvinder; Belfield, Holly; Counsell, John; Waddington, Simon N; Thomson, Emma C; Muntoni, Francesco; Breuer, Judith

Myomedin variants developed for in vitro PD-L1 diagnostics in tissue samples of non-small cell lung carcinoma patients.

为非小细胞肺癌患者组织样本中的体外 PD-L1 诊断而开发的 Myomedin 变体

Petroková Hana, Mierzwicka Joanna Maria, Chakraborty Prosenjit, Rašková Kafková Leona, Vaculová Jana, Škarda Jozef, Fischer Ondřej, Kosztyu Petr, Kuchař Milan, Raška Milan, Malý Petr

Gene therapy prevents hepatic mitochondrial dysfunction in murine deoxyguanosine kinase deficiency

基因疗法可预防小鼠脱氧鸟苷激酶缺乏症引起的肝线粒体功能障碍

Keshavan, Nandaki; Greenwood, Miriam; Prunty, Helen; Diaz, Juan Antinao; Privolizzi, Riccardo; Counsell, John; Karlsson, Anna; Sebire, Neil; Waddington, Simon; Karda, Rajvinder; Rahman, Shamima

Ascending Vaginal Infection in Mice Induces Preterm Birth and Neonatal Morbidity

小鼠上行性阴道感染可导致早产和新生儿发病率

Boyle, Ashley K; Tetorou, Konstantina; Suff, Natalie; Beecroft, Laura; Mazzaschi, Margherita; Karda, Rajvinder; Hristova, Mariya; Waddington, Simon N; Peebles, Donald

Creation of de novo cryptic splicing for ALS and FTD precision medicine

利用从头隐蔽剪接技术进行ALS和FTD精准医疗

Oscar G Wilkins ,Max Z Y J Chien # ,Josette J Wlaschin # ,Simone Barattucci ,Peter Harley ,Francesca Mattedi ,Puja R Mehta ,Maria Pisliakova ,Eugeni Ryadnov ,Matthew J Keuss ,David Thompson ,Holly Digby ,Lea Knez ,Rebecca L Simkin ,Juan Antinao Diaz ,Matteo Zanovello ,Anna-Leigh Brown ,Annalucia Darbey ,Rajvinder Karda ,Elizabeth M C Fisher ,Thomas J Cunningham ,Claire E Le Pichon ,Jernej Ule ,Pietro Fratta

Assessment of perineural spread in advanced cutaneous squamous cell carcinomas treated with immunotherapy

免疫疗法治疗晚期皮肤鳞状细胞癌的神经周围扩散评估

Cavanagh, Karda; McLean, Luke S; Lim, Annette M; Cardin, Anthony; Levy, Sidney M; Rischin, Danny

Systemic gene therapy rescues retinal dysfunction and hearing loss in a model of Norrie disease

系统性基因治疗可挽救诺里氏病模型中的视网膜功能障碍和听力丧失

Valda Pauzuolyte, Aara Patel #, James R Wawrzynski #, Neil J Ingham #, Yeh Chwan Leong, Rajvinder Karda, Maria Bitner-Glindzicz, Wolfgang Berger, Simon N Waddington, Karen P Steel, Jane C Sowden

Lessons learned from "the great mimicker disease": A retrospective study of 18 patients with scurvy

从“伟大的模仿者”坏血病中汲取的教训:一项对18例坏血病患者的回顾性研究

Miraj, Faisal; Karda, I Wayan Arya Mahendra; Abdullah, Ali; Dionysios, Eugene

Creation of de novo cryptic splicing for ALS/FTD precision medicine

为 ALS/FTD 精准医疗创建从头隐蔽剪接

Oscar G Wilkins, Max Z Y J Chien, Josette J Wlaschin, Maria Pisliakova, David Thompson, Holly Digby, Rebecca L Simkin, Juan Antinao Diaz, Puja R Mehta, Matthew J Keuss, Matteo Zanovello, Anna-Leigh Brown, Peter Harley, Annalucia Darbey, Rajvinder Karda, Elizabeth M C Fisher, Tom J Cunningham, Claire

Rapid and inexpensive purification of adenovirus vectors using an optimised aqueous two-phase technology

利用优化的水相双相技术快速、低成本地纯化腺病毒载体

Suleman, Saqlain; Schrubaji, Kuteiba; Filippou, Chrysovalanto; Ignatova, Svetlana; Hewitson, Peter; Huddleston, Jonathan; Karda, Rajvinder; Waddington, Simon N; Themis, Michael