Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome
造血干细胞基因治疗Wiskott-Aldrich综合征的疗效
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2022019117
Labrosse, Roxane; Chu, Julia I; Armant, Myriam A; Everett, John K; Pellin, Danilo; Kareddy, Niharika; Frelinger, Andrew L; Henderson, Lauren A; O'Connell, Amy E; Biswas, Amlan; Coenen-van der Spek, Jet; Miggelbrink, Alexandra; Fiorini, Claudia; Adhikari, Hriju; Berry, Charles C; Cantu, Vito Adrian; Fong, Johnson; Jaroslavsky, Jason; Karadeniz, Derin F; Li, Quan-Zhen; Reddy, Shantan; Roche, Aoife M; Zhu, Chengsong; Whangbo, Jennifer S; Dansereau, Colleen; Mackinnon, Brenda; Morris, Emily; Koo, Stephanie M; London, Wendy B; Baris, Safa; Ozen, Ahmet; Karakoc-Aydiner, Elif; Despotovic, Jenny M; Forbes Satter, Lisa R; Saitoh, Akihiko; Aizawa, Yuta; King, Alejandra; Nguyen, Mai Anh Thi; Vu, Vy Do Uyen; Snapper, Scott B; Galy, Anne; Notarangelo, Luigi D; Bushman, Frederic D; Williams, David A; Pai, Sung-Yun