Cellular and biochemical response to chaperone versus substrate reduction therapies in neuropathic Gaucher disease
神经性戈谢病对分子伴侣疗法和底物减少疗法的细胞和生化反应
期刊:PLoS One
影响因子:2.9
doi:10.1371/journal.pone.0247211
Margarita M Ivanova, Julia Dao, Neil Kasaci, Benjamin Adewale, Shaista Nazari, Lauren Noll, Jacqueline Fikry, Armaghan Hafez Sanati, Ozlem Goker-Alpan