Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity.
聚焦超声可显著扩大 AAV 递送的 Cas9 的分布和活性
期刊:Gene Therapy
影响因子:4.5
doi:10.1038/s41434-025-00517-w
Gumusgoz Emrah, Kasiri Sahba, Youssef Ibrahim, Verma Mayank, Chopra Rajiv, Villarreal Acha Daniel, Wu Jun, Marriam Ummay, Alao Esther, Chen Xin, Guisso Dikran R, Gray Steven J, Shah Bhavya R, Minassian Berge A