日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lafora disease gene therapy: EPM2A but not EPM2B overexpression results in Lafora body formation.

Lafora病基因治疗:EPM2A而非EPM2B过度表达会导致Lafora小体的形成。

Alao Esther O, Sheibani Mehrnaz, Wu Jun, Marriam Ummay, Evans Doretha, Kasiri Sahba, Verma Mayank, Nitschke Silvia, Nitschke Felix, Gray Steven J, Mitra Sharmistha, Minassian Berge A

Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity.

聚焦超声可显著扩大 AAV 递送的 Cas9 的分布和活性

Gumusgoz Emrah, Kasiri Sahba, Youssef Ibrahim, Verma Mayank, Chopra Rajiv, Villarreal Acha Daniel, Wu Jun, Marriam Ummay, Alao Esther, Chen Xin, Guisso Dikran R, Gray Steven J, Shah Bhavya R, Minassian Berge A

AAV-Mediated Artificial miRNA Reduces Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models

AAV介导的人工miRNA可减少成年多聚葡萄糖体病和拉福拉病小鼠模型中的致病性多聚葡萄糖体和神经炎症

Gumusgoz, Emrah; Kasiri, Sahba; Guisso, Dikran R; Wu, Jun; Dear, Matthew; Verhalen, Brandy; Minassian, Berge A

Targeting Gys1 with AAV-SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models

利用 AAV-SaCas9 靶向 Gys1 可减少成年多聚葡糖体病和拉福拉病小鼠模型中的致病性多聚葡糖体和神经炎症

Gumusgoz, Emrah; Guisso, Dikran R; Kasiri, Sahba; Wu, Jun; Dear, Matthew; Verhalen, Brandy; Nitschke, Silvia; Mitra, Sharmistha; Nitschke, Felix; Minassian, Berge A

Nuclease activity via self-activation and anticancer activity of a mononuclear copper(II) complex: novel role of the tertiary butyl group in the ligand frame

单核铜(II)配合物的自激活核酸酶活性和抗癌活性:配体框架中叔丁基的新作用

Ghosh, Kaushik; Kumar, Pramod; Mohan, Varun; Singh, Udai P; Kasiri, Sahba; Mandal, Subhrangsu S

Homeodomain-containing protein HOXB9 regulates expression of growth and angiogenic factors, facilitates tumor growth in vitro and is overexpressed in breast cancer tissue

含有同源结构域的蛋白HOXB9调控生长因子和血管生成因子的表达,促进体外肿瘤生长,并在乳腺癌组织中过表达。

Shrestha, Bishakha; Ansari, Khairul I; Bhan, Arunoday; Kasiri, Sahba; Hussain, Imran; Mandal, Subhrangsu S