Elucidating brain transport pathways and cell type-dependent gene silencing of a durable lipid-siRNA conjugate administered into cerebrospinal fluid.
阐明脑脊液中注入的持久性脂质-siRNA缀合物的脑运输途径和细胞类型依赖性基因沉默
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkaf600
Sorets Alexander G, Schwensen Katrina R, Francini Nora, Kjar Andrew, Abdulrahman Adam M, Shostak Alena, Katdare Ketaki A, Schoch Kathleen M, Cowell Rebecca P, Park Joshua C, Ligocki Alexander P, Ford William T, Ventura-Antunes Lissa, Hoogenboezem Ella N, Prusky Alex, Castleberry Mark, Michell Danielle L, Fritsch Emma, Lyons Sarah M, Miller Timothy M, Vickers Kasey C, Schrag Matthew S, Duvall Craig L, Lippmann Ethan S