日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Five-Year Analysis of the JULIET Trial of Tisagenlecleucel in Patients With Relapsed/Refractory Large B-Cell Lymphoma

JULIET试验中Tisagenlecleucel治疗复发/难治性大B细胞淋巴瘤患者的五年分析

Maziarz, Richard T; Bishop, Michael R; Tam, Constantine S; Borchmann, Peter; Worel, Nina; McGuirk, Joseph P; Holte, Harald; Waller, Edmund K; Jaglowski, Samantha; Andreadis, Charalambos; Foley, Stephen Ronan; Westin, Jason R; Fleury, Isabelle; Ho, P Joy; Mielke, Stephan; Teshima, Takanori; Janakiram, Murali; Hsu, Jingmei; Izutsu, Koji; Kersten, Marie José; Ghosh, Monalisa; Wagner-Johnston, Nina; Kato, Koji; Corradini, Paolo; Ma, Wanying; Han, Xia; Nuortti, Marja; Awasthi, Rakesh; Mundt, Kirsten E; Majdan, Marta; Maier, Harald J; Jegerlehner, Andrea; Salles, Gilles; Schuster, Stephen J

Investigation of Profile-Related Evidence Determining Individualized Cancer Therapy (I-PREDICT) N-of-1 Precision Oncology Study: Molecular Profiling to Match Individually Dosed, Personalized Drug Combinations

基于分子谱分析确定个体化癌症治疗的证据调查(I-PREDICT)N-of-1精准肿瘤学研究:分子谱分析匹配个体化给药的个性化药物组合

Sicklick, Jason K; Nishizaki, Daisuke; Miyashita, Hirotaka; Okamura, Ryosuke; Hahn, Michael E; Nikanjam, Mina; Fanta, Paul T; Piccioni, David E; Patel, Hitendra; Eskander, Ramez N; McKay, Rana R; Ross, Jeffrey S; Lee, J Jack; Lippman, Scott M; Kato, Shumei; Kurzrock, Razelle

Implementing generative artificial intelligence in precision oncology: safety, governance, and significance

在精准肿瘤学中应用生成式人工智能:安全性、治理和意义

Hamamoto, Ryuji; Koyama, Takafumi; Takahashi, Satoshi; Yasuda, Tomohiro; Kobayashi, Kazuma; Akagi, Yu; Kouno, Nobuji; Sudo, Kazuki; Hirata, Makoto; Sunami, Kuniko; Kubo, Takashi; Katayama, Hiroshi; Takashima, Atsuo; Taniguchi, Tomonori; Matsumoto, Hiromi; Shibaki, Ryota; Asada, Ken; Komatsu, Masaaki; Kaneko, Syuzo; Yamada, Masayoshi; Horinouchi, Hidehito; Tanaka, Katsuya; Goto, Yasushi; Kato, Ken; Saito, Yutaka; Nakamura, Kenichi; Yamamoto, Noboru

Guanine nucleotides drive ribosome biogenesis and glycolytic reprogramming in acute myeloid leukemia stem cells

鸟嘌呤核苷酸驱动急性髓系白血病干细胞中的核糖体生物合成和糖酵解重编程

Kawano, Gentaro; Ikeda, Riichiro; Ishihara, Daisuke; Shima, Takahiro; Sakoda, Teppei; Yamamoto, Shunsuke; Kochi, Yu; Semba, Yuichiro; Ashitani, Sanae; Mori, Yasuo; Kato, Koji; Maeda, Takahiro; Miyamoto, Toshihiro; Soga, Tomoyoshi; Akashi, Koichi; Kikushige, Yoshikane

Orbitofrontal cortex drives predictive filtering of sensory responses.

眶额皮层驱动感觉反应的预测性过滤。

Tsukano Hiroaki, Garcia Michellee M, Dandu Pranathi R, Kato Hiroyuki K

OMG! A proteomic determinant of neurodegenerative resiliency

我的天!神经退行性疾病恢复力的蛋白质组学决定因素

Duggan, Michael R; Oh, Hamilton Se-Hwee; Frank, Philipp; Gomez, Gabriela T; Zweibaum, David; Cui, Yuhan; Chen, Jingsha; Surapaneni, Aditya; Blew, Cassandra O; Dark, Heather E; Joynes, Cassandra M; Kandala, Sridhar; Bilgel, Murat; Farinas, Amelia; Erus, Guray; Tian, Qu; Candia, Julián; Pucha, Krishna A; Landman, Bennett A; Dumitrescu, Logan; Hohman, Timothy J; Lewis, Alexandria; Moghekar, Abhay; Siavoshi, Fatemeh; Ali, Muhammad; Liu, Menghan; Xu, Ying; Western, Daniel; Kaneko, Naoto; Kato, Shintaro; Furuichi, Makio; Shibayama, Masaki; Katsuno, Masahisa; Nishita, Yukiko; Otsuka, Rei; Gottesman, Rebecca F; Dammer, Eric B; Seyfried, Nicholas T; Levey, Allan I; B Johnson, Erik C; Mormino, Elizabeth; Wagner, Anthony D; Poston, Kathleen L; Kapogiannis, Dimitrios; Grams, Morgan E; Bhargava, Pavan; Waga, Iwao; Davatzikos, Christos; Resnick, Susan M; Ferrucci, Luigi; Bennett, David A; Cruchaga, Carlos; Wyss-Coray, Tony; Kivimäki, Mika; Coresh, Josef; Walker, Keenan A

A Nonviral Neo-Nucleocapsid for Cell-Specific RNA Delivery Developed by Pseudo-Cyclic Peptide Grafting and Directed Evolution

利用伪环肽嫁接和定向进化技术开发了一种用于细胞特异性RNA递送的非病毒新核衣壳

Kanayama, Daiki; Terasaka, Naohiro; Kato, Kazuki; Okazaki, Sae; Suga, Hiroaki

Microglia Display Heterogeneous Initial Responses to Disseminated Tumor Cells

小胶质细胞对播散性肿瘤细胞表现出异质性初始反应

Tsuji, Takahiro; Hirose, Haruka; Sugiyama, Daisuke; Shindo, Mariko; Hartantyo, Rahadian Yudo; Saito, Yutaro; Tatematsu, Tsuyako; Sugio, Shouta; Sanbo, Makoto; Hirabayashi, Masumi; Kojima, Yasuhiro; Koseki, Jun; Hosoya, Kazutaka; Yoshida, Hiroshi; Ogimoto, Tatsuya; Yasuda, Yuto; Hashimoto, Kentaro; Ajimizu, Hitomi; Sakamori, Yuichi; Yoshida, Hironori; Sano, Noritaka; Tanji, Masahiro; Ito, Hiroaki; Terada, Kazuhiro; Hamaji, Masatsugu; Menju, Toshi; Konishi, Hiroyuki; Kumagai, Shogo; Ghajar, Cyrus M; Kato, Daisuke; Date, Hiroshi; Yoshizawa, Akihiko; Arakawa, Yoshiki; Ozasa, Hiroaki; Moorhouse, Andrew J; Shimamura, Teppei; Nishikawa, Hiroyoshi; Hirai, Toyohiro; Wake, Hiroaki