日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Potential effects of endogenous RNA/DNA hybrids on CRISPR-Cas9-mediated homology-directed repair.

内源性 RNA/DNA 杂交体对 CRISPR-Cas9 介导的同源定向修复的潜在影响。

Puzzo Francesco, Bayram Batuhan, Macaubas Claudia, Lin Angela, Jang Hagoon, Zhang Feijie, Mellins Elizabeth, Kay Mark A

Genome engineering with Cas9 and AAV repair templates generates frequent concatemeric insertions of viral vectors

利用Cas9和AAV修复模板进行基因组工程会产生频繁的病毒载体串联插入。

Suchy, Fabian P; Karigane, Daiki; Nakauchi, Yusuke; Higuchi, Maimi; Zhang, Jinyu; Pekrun, Katja; Hsu, Ian; Fan, Amy C; Nishimura, Toshinobu; Charlesworth, Carsten T; Bhadury, Joydeep; Nishimura, Toshiya; Wilkinson, Adam C; Kay, Mark A; Majeti, Ravindra; Nakauchi, Hiromitsu

Stereo-random oligonucleotides enable efficient recruitment of ADAR in vitro and in vivo

立体随机寡核苷酸能够高效地在体外和体内募集ADAR。

Pfeiffer, Laura S; Merkle, Tobias; Vogel, Paul; Jarmoskaite, Inga; Geisinger, Jonathan M; Latifi, Ngadhnjim; Herrera-Barrera, Marco; Zhang, Feijie; Groß, Lisa; Schlitz, Carolin; Hofacker, Daniel T; Lochmann, Clemens; Fumagalli, Davide; Gackstatter, Stefanie; Deisling, Vanessa; Kay, Mark A; Li, Jin Billy; Stafforst, Thorsten

The deLIVERed promises of gene therapy: Past, present, and future of liver-directed gene therapy

基因疗法的已实现承诺:肝脏靶向基因疗法的过去、现在和未来

Puzzo, Francesco; Kay, Mark A

Low-level shRNA Cytotoxicity Can Contribute to MYC-induced Hepatocellular Carcinoma in Adult Mice

低水平shRNA细胞毒性可导致成年小鼠MYC诱导的肝细胞癌

Beer, Shelly; Bellovin, David I; Lee, Joyce S; Komatsubara, Kimberly; Wang, Lora S; Koh, Huishan; Börner, Kathleen; Storm, Theresa A; Davis, Corrine R; Kay, Mark A; Felsher, Dean W; Grimm, Dirk

Reprogramming AAV tropism with tumor-associated targeting ligands

利用肿瘤相关靶向配体重编程AAV嗜性

Trisno, Stephen L; Kay, Mark A

Development of a novel gene editing lexicon for hemophilia: methodology and results

开发用于血友病的新型基因编辑词汇表:方法和结果

Kessler, Craig M; Valentino, Leonard A; Thornburg, Courtney D; Unzu, Carmen; Kay, Mark A; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; McKeown, William; Pierce, Glenn F; Khair, Kate; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Sindhurakar, Anil; Whyte, Lauren; Delwart, Virginie; Chiao, Megan; Gutstein, David E; Antonino, Ilia; Hermans, Cedric; Pipe, Steven W

Ruvkun and Ambros recognized for miRNAs

Ruvkun 和 Ambros 因 miRNA 而受到认可

Kay, Mark A

A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results

针对血友病群体的新型基因编辑词汇策略:研发计划及初步结果

Hermans, Cedric; Valentino, Leonard A; Thornburg, Courtney D; Unzu, Carmen; Kay, Mark A; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; McKeown, William; Pierce, Glenn F; Khair, Kate; Pipe, Steven W; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Chiao, Megan; Antonino, Ilia; Kessler, Craig

A standardized ontology for naming tRNA-derived RNAs based on molecular origin

基于分子起源的tRNA衍生RNA命名标准化本体

Holmes, Andrew D; Chan, Patricia P; Chen, Qi; Ivanov, Pavel; Drouard, Laurence; Polacek, Norbert; Kay, Mark A; Lowe, Todd M