Transient expression of an adenine base editor corrects the Hutchinson-Gilford progeria syndrome mutation and improves the skin phenotype in mice
腺嘌呤碱基编辑器的瞬时表达可纠正哈钦森-吉尔福德早衰综合征突变并改善小鼠的皮肤表型
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-022-30800-y
Daniel Whisenant #, Kayeong Lim #, Gwladys Revêchon, Haidong Yao, Martin O Bergo, Piotr Machtel, Jin-Soo Kim, Maria Eriksson