Phase Ib study of PRT543, an oral protein arginine methyltransferase 5 (PRMT5) inhibitor, in patients with advanced splicing factor-mutant myeloid malignancies
PRT543(一种口服蛋白精氨酸甲基转移酶 5 (PRMT5) 抑制剂)治疗晚期剪接因子突变型髓系恶性肿瘤患者的 Ib 期研究
期刊:Leukemia
影响因子:13.4
doi:10.1038/s41375-025-02515-8
Bewersdorf, Jan Philipp; Mi, Xiaoli; Lu, Bin; Kuykendall, Andrew; Sallman, David; Patel, Manish; Stevens, Don; Philipovskiy, Alexander; Sutamtewagul, Grerk; Masarova, Lucia; Keiffer, Gina; Verma, Amit; Bhagwat, Neha; Wang, Min; Moore, Andrew; Rager, Joseph; Heiser, Diane; Ro, Sunhee; Hong, Wan-Jen; Abdel-Wahab, Omar; Stein, Eytan M