MeCP2 gene therapy ameliorates disease phenotype in mouse model for Pitt Hopkins syndrome
MeCP2 基因疗法改善皮特霍普金斯综合征小鼠模型的疾病表型
期刊:Neurotherapeutics
影响因子:5.6
doi:10.1016/j.neurot.2024.e00376
Cassandra N Dennys, Sheryl Anne D Vermudez, Robert J M Deacon, J Andrea Sierra-Delgado, Kelly Rich, Xiaojin Zhang, Aditi Buch, Kelly Weiss, Yuta Moxley, Hemangi Rajpal, Francisca D Espinoza, Samantha Powers, Ariel S Ávila, Rocco G Gogliotti, Patricia Cogram, Colleen M Niswender, Kathrin C Meyer