日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Divalent siRNA for prion disease

用于朊病毒病的二价siRNA

Gentile, Juliana E; Corridon, Taylor L; Serack, Fiona E; Echeverria, Dimas; Kennedy, Zachary C; Gallant-Behm, Corrie L; Hassler, Matthew R; Kinberger, Garth A; Kelemen, Margaret N; Kamath, Nikita G; Lian, Yuan; Gross, Katherine Y; Miller, Rachael; DeSouza-Lenz, Kendrick; Howard, Michael; Guzman, Kenia; Chan, Nathan; Laversenne, Vanessa; Curtis, Daniel; Fettes, Kevin; Lemaitre, Marc; Jackson, Aimee L; Yamada, Ken; Alterman, Julia F; Coffey, Alissa A; Minikel, Eric Vallabh; Khvorova, Anastasia; Vallabh, Sonia M

Divalent siRNA for prion disease.

用于朊病毒病的二价siRNA。

Gentile Juliana E, Corridon Taylor L, Serack Fiona E, Echeverria Dimas, Kennedy Zachary C, Gallant-Behm Corrie L, Hassler Matthew R, Kinberger Garth A, Kelemen Margaret N, Kamath Nikita G, Lian Yuan, Gross Katherine Y, Miller Rachael, DeSouza-Lenz Kendrick, Howard Michael, Guzman Kenia, Chan Nathan, Laversenne Vanessa, Curtis Daniel T, Fettes Kevin, Lemaitre Marc, Jackson Aimee L, Yamada Ken, Alterman Julia F, Coffey Alissa A, Minikel Eric Vallabh, Khvorova Anastasia, Vallabh Sonia M

Single-dose administration of therapeutic divalent siRNA targeting MECP2 prevents lethality for one year in an MECP2 duplication mouse model

单次注射靶向 MECP2 的治疗性二价 siRNA 可使 MECP2 重复小鼠模型免于死亡一年。

Hariharan, Vignesh N; Summers, Ashley; Clipperton-Allen, Amy E; Caiazzi, Jillian; Hildebrand, Samuel R; O'Reilly, Daniel; Tang, Qi; Kennedy, Zachary; Echeverria, Dimas; McHugh, Nicholas; Cooper, David; Souza, Jacqueline; Ferguson, Chantal; Bogdanik, Laurent; Coenraads, Monica; Khvorova, Anastasia

An interdisciplinary framework of youth participatory action research informed by curricula, youth, adults, and researchers

以课程、青少年、成人和研究人员为指导的青少年参与式行动研究跨学科框架

Leman, Amy M; Dariotis, Jacinda K; Markazi, Daniela M; Kennedy, Zachary; Tracy, Mynda; Park, Ye Rang; Griffith, Aisha N

Identification of selective and non-selective C9ORF72 targeting in vivo active siRNAs

鉴定选择性和非选择性靶向C9ORF72的体内活性siRNA

Gilbert, James W; Kennedy, Zachary; Godinho, Bruno M D C; Summers, Ashley; Weiss, Alexandra; Echeverria, Dimas; Bramato, Brianna; McHugh, Nicholas; Cooper, David; Yamada, Ken; Hassler, Matthew; Tran, Hélène; Gao, Fen Biao; Brown, Robert H Jr; Khvorova, Anastasia

Di-valent siRNA-mediated silencing of MSH3 blocks somatic repeat expansion in mouse models of Huntington's disease

二价siRNA介导的MSH3沉默可阻断亨廷顿病小鼠模型中的体细胞重复序列扩增

O'Reilly, Daniel; Belgrad, Jillian; Ferguson, Chantal; Summers, Ashley; Sapp, Ellen; McHugh, Cassandra; Mathews, Ella; Boudi, Adel; Buchwald, Julianna; Ly, Socheata; Moreno, Dimas; Furgal, Raymond; Luu, Eric; Kennedy, Zachary; Hariharan, Vignesh; Monopoli, Kathryn; Yang, X William; Carroll, Jeffery; DiFiglia, Marian; Aronin, Neil; Khvorova, Anastasia

Imaging Net Retrograde Axonal Transport In Vivo: A Physiological Biomarker.

体内逆行轴突净运输成像:一种生理生物标志物

Lee Pin-Tsun Justin, Kennedy Zachary, Wang Yuzhen, Lu Yimeng, Cefaliello Carolina, Uyan Özgün, Song Chun-Qing, Godinho Bruno Miguel da Cruz, Xu Zuoshang, Rusckowski Mary, Xue Wen, Brown Robert H Jr

The Promise of Emergent Nanobiotechnologies for In Vivo Applications and Implications for Safety and Security

新兴纳米生物技术在体内应用中的前景及其对安全性的影响

Arnold, Anne M; Bradley, Ashley M; Taylor, Karen L; Kennedy, Zachary C; Omberg, Kristin M

Intrathecal Delivery of Therapeutic Oligonucleotides for Potent Modulation of Gene Expression in the Central Nervous System

鞘内注射治疗性寡核苷酸以强效调节中枢神经系统基因表达

Kennedy, Zachary; Gilbert, James W; Godinho, Bruno M D C

Systematic determination of the relationship between nanoparticle core diameter and toxicity for a series of structurally analogous gold nanoparticles in zebrafish

系统测定斑马鱼体内一系列结构类似的金纳米颗粒的核径与毒性之间的关系

Truong, Lisa; Zaikova, Tatiana; Baldock, Brandi L; Balik-Meisner, Michele; To, Kimberly; Reif, David M; Kennedy, Zachary C; Hutchison, James E; Tanguay, Robert L