日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Rational design of base, sugar and backbone modifications improves ADAR-mediated RNA editing

碱基、糖和骨架修饰的合理设计改善了ADAR介导的RNA编辑

Genliang Lu, Chikdu Shivalila, Prashant Monian, Hui Yu, Ian Harding, Stearne Briem, Michael Byrne, Alyse Faraone, Stephen Friend, Olivia Huth, Naoki Iwamoto, Tomomi Kawamoto, Jayakanthan Kumarasamy, Anthony Lamattina, Kenneth Longo, Leah McCarthy, Andrew McGlynn, Allison Molski, Qianli Pan, Tom Pu, 

Variant-selective stereopure oligonucleotides protect against pathologies associated with C9orf72-repeat expansion in preclinical models

变体选择性立体纯寡核苷酸可在临床前模型中预防与 C9orf72 重复扩增相关的病理

Yuanjing Liu #, Jean-Cosme Dodart #, Helene Tran #, Shaunna Berkovitch, Maurine Braun, Michael Byrne, Ann F Durbin, Xiao Shelley Hu, Naoki Iwamoto, Hyun Gyung Jang, Pachamuthu Kandasamy, Fangjun Liu, Kenneth Longo, Jörg Ruschel, Juili Shelke, Hailin Yang, Yuan Yin, Amy Donner, Zhong Zhong, Chandra V