GAA replacement improves respiratory muscle, neural, and alveolar pathology in the pompe mouse.
GAA 替代疗法可改善庞贝氏症小鼠的呼吸肌、神经和肺泡病理
期刊:Respiratory Physiology & Neurobiology
影响因子:1.6
doi:10.1016/j.resp.2025.104433
Roger Angela L, El Haddad Lea, Huston Meredith L, Kehoe Sean, Le Davina, Khan Mainur, Scarrow Evelyn, Gonzalez Trevor, Benkert Abigail, Asokan Aravind, ElMallah Mai K