日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Structural characterization of antibody-responses following Zolgensma treatment for AAV capsid engineering to expand patient cohorts.

对Zolgensma治疗后抗体反应的结构进行表征,以进行AAV衣壳工程改造,从而扩大患者群体

Mietzsch Mario, Hsi Jane, Nelson Austin R, Khandekar Neeta, Huang Ann-Maree, Smith Nicholas Jc, Zachary Jon, Potts Lindsay, Farrar Michelle A, Chipman Paul, Ghanem Mohammad, Alexander Ian E, Logan Grant J, Huiskonen Juha T, McKenna Robert

Structural characterization of antibody-responses from Zolgensma treatment provides the blueprint for the engineering of an AAV capsid suitable for redosing

对Zolgensma治疗后抗体反应的结构表征为设计适用于重复给药的AAV衣壳提供了蓝图。

Mietzsch, Mario; Nelson, Austin R; Hsi, Jane; Zachary, Jon; Potts, Lindsay; Chipman, Paul; Ghanem, Mohammad; Khandekar, Neeta; Alexander, Ian E; Logan, Grant J; Huiskonen, Juha T; McKenna, Robert

Use of a Hybrid Adeno-Associated Viral Vector Transposon System to Deliver the Insulin Gene to Diabetic NOD Mice

利用混合腺相关病毒载体转座子系统将胰岛素基因递送至糖尿病NOD小鼠

La, Que T; Ren, Binhai; Logan, Grant J; Cunningham, Sharon C; Khandekar, Neeta; Nassif, Najah T; O'Brien, Bronwyn A; Alexander, Ian E; Simpson, Ann M

Cold exposure promotes obesity and impairs glucose homeostasis in mice subjected to a high‑fat diet.

寒冷刺激会促进高脂饮食小鼠的肥胖,并损害其葡萄糖稳态

Zhu Ping, Zhang Zhi-Hui, Huang Xu-Feng, Shi Yan-Chuan, Khandekar Neeta, Yang He-Qin, Liang Shi-Yu, Song Zhi-Yuan, Lin Shu

RANKL Reduces Body Weight and Food Intake via the Modulation of Hypothalamic NPY/CART Expression

RANKL通过调节下丘脑NPY/CART表达来降低体重和食物摄入量

Zhu, Ping; Zhang, Zhihui; Huang, Xufeng; Liang, Shiyu; Khandekar, Neeta; Song, Zhiyuan; Lin, Shu