Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model
细胞穿透肽偶联的剪接转换寡核苷酸可减轻BTK/Tec双缺陷型X连锁无丙种球蛋白血症模型中的表型
期刊:RSC Chemical Biology
影响因子:3.1
doi:10.1039/d4cb00312h
Bestas, Burcu; Estupiñán, H Yesid; Wang, Qing; Kharazi, Shabnam; He, Chenfei; K Mohammad, Dara; Gupta, Dhanu; Wiklander, Oscar P B; Lehto, Taavi; Lundin, Karin E; Berglöf, Anna; Karlsson, Mikael C I; Abendroth, Frank; El Andaloussi, Samir; Gait, Michael J; Wood, Matthew J A; Leumann, Christian J; Stetsenko, Dmitry A; Månsson, Robert; Wengel, Jesper; Zain, Rula; Smith, C I Edvard