日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

International Consensus-Driven Recommendations for Patient-Reported Outcome Research Objectives in Early Phase Dose-Finding Oncology Trials: OPTIMISE-ROR

早期剂量探索性肿瘤试验中患者报告结局研究目标的国际共识驱动建议:OPTIMISE-ROR

Alger, Emily; Aiyegbusi, Olalekan Lee; Dueck, Amylou C; Minchom, Anna; Pe, Madeline; Peipert, John D; Snyder, Claire; Symeonides, Stefan N; Wilson, Roger; Basch, Ethan; Qiao, Yu; Bates, Susan E; Bulbeck, Helen; Dean, Lizzie; Di Maio, Massimo; Hansen, Aaron R; Kholmanskikh, Olga; Kobayashi, Ken; Landers, Dónal; Le Tourneau, Christophe; Lee, J Jack; Ma, Brigette B Y; Marshall, Lynley V; Patel, Sheetal; Petrie, Joan; Pond, Gregory R; Prior, Kieran; Rantell, Khadija R; Reeve, John F; Solovyeva, Olga; Wages, Nolan A; Weber, Harald A; Calvert, Melanie J; Yap, Christina

SPIRIT-DEFINE explanation and elaboration: recommendations for enhancing quality and impact of early phase dose-finding clinical trials protocols

SPIRIT-DEFINE 解释和阐述:提高早期剂量探索临床试验方案质量和影响的建议

Ursino, Moreno; Villacampa, Guillermo; Rekowski, Jan; Dimairo, Munyaradzi; Solovyeva, Olga; Ashby, Deborah; Berlin, Jordan; Boix, Oliver; Calvert, Melanie; Chan, An-Wen; Coschi, Courtney H; Evans, Thomas R Jeffry; Garrett-Mayer, Elizabeth; Golub, Robert M; Guo, Christina; Hayward, Kathryn S; Hopewell, Sally; Isaacs, John D; Ivy, S Percy; Jaki, Thomas; Kholmanskikh, Olga; Kightley, Andrew; Lee, Shing; Liu, Rong; Mander, Adrian; Marshall, Lynley V; Matcham, James; Patel, Dhrusti; Peck, Richard; Rantell, Khadija Rerhou; Richards, Dawn P; Rouhifard, Mahtab; Seymour, Lesley; Tanaka, Yoshiya; Weir, Christopher J; de Bono, Johann; Yap, Christina

CONSORT-DEFINE explanation and elaboration: recommendations for enhancing reporting quality and impact of early phase dose-finding clinical trials

CONSORT-DEFINE 解释和阐述:提高早期剂量探索临床试验报告质量和影响的建议

Rekowski, Jan; Guo, Christina; Solovyeva, Olga; Dimairo, Munyaradzi; Rouhifard, Mahtab; Patel, Dhrusti; Alger, Emily; Ashby, Deborah; Berlin, Jordan; Boix, Oliver; Calvert, Melanie; Chan, An-Wen; Coschi, Courtney H; de Bono, Johann; Evans, Thomas R Jeffry; Garrett-Mayer, Elizabeth; Golub, Robert M; Hayward, Kathryn S; Hopewell, Sally; Isaacs, John D; Ivy, S Percy; Jaki, Thomas; Kholmanskikh, Olga; Kightley, Andrew; Lee, Shing; Liu, Rong; Maia, Israel; Mander, Adrian; Marshall, Lynley V; Matcham, James; Peck, Richard; Rantell, Khadija Rerhou; Richards, Dawn P; Seymour, Lesley; Tanaka, Yoshiya; Ursino, Moreno; Weir, Christopher J; Yap, Christina

Advancing patient-centric care: integrating patient reported outcomes for tolerability assessment in early phase clinical trials - insights from an expert virtual roundtable

推进以患者为中心的医疗服务:将患者报告结局纳入早期临床试验耐受性评估——专家虚拟圆桌会议的见解

Yap, Christina; Lee Aiyegbusi, Olalekan; Alger, Emily; Basch, Ethan; Bell, Jill; Bhatnagar, Vishal; Cella, David; Collis, Philip; Dueck, Amylou C; Gilbert, Alexandra; Gnanasakthy, Ari; Greystoke, Alastair; Hansen, Aaron R; Kamudoni, Paul; Kholmanskikh, Olga; King-Kallimanis, Bellinda L; Krumholz, Harlan; Minchom, Anna; O'Connor, Daniel; Petrie, Joan; Piccinin, Claire; Rantell, Khadija Rerhou; Rauz, Saaeha; Retzer, Ameeta; Rizk, Steven; Wagner, Lynne; Sasseville, Maxime; Seymour, Lesley K; Weber, Harald A; Wilson, Roger; Calvert, Melanie; Peipert, John Devin

Activation of RhoC by regulatory ubiquitination is mediated by LNX1 and suppressed by LIS1

RhoC 的激活是通过 LNX1 介导的调控性泛素化实现的,并受到 LIS1 的抑制。

Stanislav Kholmanskikh,Shawn Singh,M Elizabeth Ross

Postzygotic inactivating mutations of RHOA cause a mosaic neuroectodermal syndrome

RHOA 的合子后失活突变导致马赛克神经外胚层综合征

Pierre Vabres #, Arthur Sorlin #, Stanislav S Kholmanskikh #, Bénédicte Demeer, Judith St-Onge, Yannis Duffourd, Paul Kuentz, Jean-Benoît Courcet, Virginie Carmignac, Philippine Garret, Didier Bessis, Odile Boute, Alain Bron, Guillaume Captier, Esther Carmi, Bernard Devauchelle, David Geneviève, Cat

De novo CCND2 mutations leading to stabilization of cyclin D2 cause megalencephaly-polymicrogyria-polydactyly-hydrocephalus syndrome

新生CCND2基因突变导致细胞周期蛋白D2稳定,引起巨脑畸形-多小脑回畸形-多指畸形-脑积水综合征。

Ghayda Mirzaa # ,David A Parry # ,Andrew E Fry # ,Kristin A Giamanco # ,Jeremy Schwartzentruber ,Megan Vanstone ,Clare V Logan ,Nicola Roberts ,Colin A Johnson ,Shawn Singh ,Stanislav S Kholmanskikh ,Carissa Adams ,Rebecca D Hodge ,Robert F Hevner ,David T Bonthron ,Kees P J Braun ,Laurence Faivre ,Jean-Baptiste Rivière ,Judith St-Onge ,Karen W Gripp ,Grazia Ms Mancini ,Ki Pang ,Elizabeth Sweeney ,Hilde van Esch ,Nienke Verbeek ,Dagmar Wieczorek ,Michelle Steinraths ,Jacek Majewski ,Daniela T Pilz ,M Elizabeth Ross ,William B Dobyns ,Eamonn G Sheridan

LRP6 exerts non-canonical effects on Wnt signaling during neural tube closure

LRP6 在神经管闭合过程中对 Wnt 信号发挥非典型作用

Jason D Gray, Stanislav Kholmanskikh, Bozena S Castaldo, Alex Hansler, Heekyung Chung, Brian Klotz, Shawn Singh, Anthony M C Brown, M Elizabeth Ross

LRP6 exerts non-canonical effects on Wnt signaling during neural tube closure

LRP6在神经管闭合过程中对Wnt信号通路发挥非经典作用

Jason D Gray,Stanislav Kholmanskikh, Bozena S Castaldo, Alex Hansler, Heekyung Chung, Brian Klotz, Shawn Singh, Anthony M C Brown, M Elizabeth Ross

De novo mutations in the actin genes ACTB and ACTG1 cause Baraitser-Winter syndrome

肌动蛋白基因 ACTB 和 ACTG1 的新生突变导致 Baraitser-Winter 综合征

Jean-Baptiste Rivière, Bregje W M van Bon, Alexander Hoischen, Stanislav S Kholmanskikh, Brian J O'Roak, Christian Gilissen, Sabine Gijsen, Christopher T Sullivan, Susan L Christian, Omar A Abdul-Rahman, Joan F Atkin, Nicolas Chassaing, Valerie Drouin-Garraud, Andrew E Fry, Jean-Pierre Fryns, Karen