Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or B
菲图西兰预防性治疗及围手术期管理在A型或B型血友病患者中的长期安全性和有效性
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2024013900
Pipe, Steven W; Lissitchkov, Toshko; Georgiev, Pencho; Mangles, Sarah; Hegemann, Inga; Trinchero, Alice; Chowdary, Pratima; Forbes, Adam; Feng, Liqi; Menapace, Laurel A; Kichou, Salim; Andersson, Shauna; Demissie, Marek; Ragni, Margaret V