Safety and efficacy of MCO-010 optogenetic therapy in patients with Stargardt disease in USA (STARLIGHT): an open-label multi-center Ph2 trial
MCO-010 光遗传疗法在美国治疗 Stargardt 病患者的安全性和有效性（STARLIGHT）：一项开放标签、多中心 II 期临床试验
期刊:EClinicalMedicine
影响因子:10
doi:10.1016/j.eclinm.2025.103430
Lam, Byron L; Zak, Vitaliy; Gonzalez, Victor H; Gregori, Ninel Z; Chavala, Sai H; Batabyal, Subrata; Carlson, Michael; Kim, Sanghoon; Ayyagari, Ananta; Chang, Jean; Lane, Hayley; Choudry, Nozhat; Koester, John; Von Tress, Mark; Piltz-Seymour, Jody; Sharif, Najam A; Tsang, Stephen H; Mahajan, Vinit B; Boyer, David S; Ho, Allen C; Barone, Samuel B; Mohanty, Samarendra K
