AAV9-mediated KCNH2 suppression-replacement gene therapy in a transgenic rabbit model of type 1 short QT syndrome
在1型短QT综合征转基因兔模型中,AAV9介导的KCNH2抑制替代基因疗法
期刊:European Heart Journal
影响因子:
doi:10.1093/eurheartj/ehaf660
Nimani, Saranda; Bains, Sahej; Alerni, Nicolò; Ördög, Balázs; Horváth, András; Matas, Lluis; Louradour, Julien; Giammarino, Lucilla; Tester, David J; Beslac, Olgica; Lopez, Ruben; Meier, Stefan; Egle, Manuel; Christoforou, Nicolas; Barbieri, Miriam; Vashanthakumar, Varjany; Perez-Feliz, Stefanie; Parodi, Chiara; Garcia Casalta, Luisana G; Kim, C S John; Zhou, Wei; Ye, Dan; Jurgensen, Jacqulyn; Barry, Michael A; Bego, Mariana; Keyes, Lisa; Owens, Jane; Pinkstaff, Jason; Christoph, Jan; Zehender, Manfred; Brunner, Michael; Heijman, Jordi; Casoni, Daniela; Praz, Fabien; Haeberlin, Andreas; Brooks, Gabriel; Ackerman, Michael J; Odening, Katja E