日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Novel transferrin receptor-mediated enzyme replacement therapy efficiently treats myogenic and neurogenic aspects of Pompe disease in mice.

新型转铁蛋白受体介导的酶替代疗法可有效治疗小鼠庞贝病的肌源性和神经源性方面

George Kelly, Riley Raquel, Zhou Shan, Allen Elizabeth, Smith Laurie, Kistanova Elena, Kinton Sofia, Guo Lilu, Bangari Dinesh, Ismail Ayman, Thummapudi Jayaprakash, Boumezbeur Fawzi, Selingue Erwan, Tamarelle Dorothée, Capdevila Cecile, Do Tuan-Minh, Lesuisse Dominique, Leksa Nina, Sardi Pablo, van der Flier Arjan

Elovl1 inhibition reduced very long chain fatty acids in a mouse model of adrenoleukodystrophy.

Elovl1 抑制剂可降低肾上腺脑白质营养不良小鼠模型中的极长链脂肪酸含量

Huang Jeremy Y, Freed Brian, Hanus Martin, Keefe Kelly, Chiang Ming Sum Ruby, Brezzani Alexander, Luo Yongyi, Li Yihang, Lam Becky, Holley Stephanie, Gans Joseph, Dostalova Zuzana, Tang Buyun, Phaneuf Clifford, Teeple Erin, Parisi Laura, Guo Lilu, Zhao Zhonglin, Kinton Sofia N, Dwyer Jacquelyn, Teixeira Sandrine, Ma Hong, Asmussen Gary, McLaren Rajashree, Wang Donghui, Baker Ann, Siegel Craig S, Fink David, Randall Kristen, Belenky Alexei, Venugopal Suchitra, Gaglia Giorgio, Johnson Jennifer, Bangari Dinesh S, Zhang Bailin, Michel Alexander, Proto Jonathan D, Kloss Alla, Sardi S Pablo, Gladysheva Tatiana, Kayatekin Can