Safer and efficient base editing and prime editing via ribonucleoproteins delivered through optimized lipid-nanoparticle formulations
通过优化的脂质纳米颗粒制剂递送核糖核蛋白,实现更安全高效的碱基编辑和先导编辑
期刊:Nature Biomedical Engineering
影响因子:26.8
doi:10.1038/s41551-024-01296-2
Rafał Hołubowicz #,Samuel W Du #,Jiin Felgner #,Roman Smidak,Elliot H Choi,Grazyna Palczewska,Carolline Rodrigues Menezes,Zhiqian Dong,Fangyuan Gao,Omar Medani,Alexander L Yan,Maria W Hołubowicz,Paul Z Chen,Marco Bassetto,Eleonora Risaliti,David Salom,J Noah Workman,Philip D Kiser,Andrzej T Foik,David C Lyon,Gregory A Newby,David R Liu,Philip L Felgner,Krzysztof Palczewski