日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Effect of COVID19 pandemic on Argentinian Fabry and Gaucher patients

新冠疫情对阿根廷法布里病和戈谢病患者的影响

Arnold, Georgianne L; Yester, Jessie; McCracken, Elizabeth; Feingold, Brian D; Vockley, Jerry; Oliveira, Maria Carolina FA; Yund, Brianna D; Grant, Nathan; Eisengart, Julie B; Giugliani, Roberto; González-Lamuño, Domingo; Aldamiz-Echevarría, Luis; Pintos-Morell, Guillem; Toscano, Antonio; Scarpa, Maurizio; Parini, Rossella; Donati, Alice; Crescimanno, Grazia; Fiumara, Agata; Fischetto, Rita; Gasperini, Serena; Siciliano, Gabriele; Ravaglia, Sabrina; Sechi, Annalisa; Piperno, Alberto; Cianci, Vittorio; Maggi, Lorenzo; Musumeci, Olimpia; Taurisano, Roberta; Verrecchia, Elena; Rozenfeld, Paula A; Kisinovsky, Isaac

Neuro-Otological and Peripheral Nerve Involvement in Fabry Disease

法布里病中的神经耳科和周围神经受累

Carmona, Sergio; Weinschelbaum, Romina; Pardal, Ana; Marchesoni, Cintia; Zuberbuhler, Paz; Acosta, Patricia; Cáceres, Guillermo; Kisinovsky, Isaac; Bayón, Luciana; Reisin, Ricardo

Velaglucerase alfa (VPRIV) enzyme replacement therapy in patients with Gaucher disease: Long-term data from phase III clinical trials

戈谢病患者接受维拉葡糖苷酶α (VPRIV) 酶替代疗法:来自 III 期临床试验的长期数据

Hughes, Derralynn A; Gonzalez, Derlis E; Lukina, Elena A; Mehta, Atul; Kabra, Madhulika; Elstein, Deborah; Kisinovsky, Isaac; Giraldo, Pilar; Bavdekar, Ashish; Hangartner, Thomas N; Wang, Nan; Crombez, Eric; Zimran, Ari