A phase 2 randomized, double-blind trial of ART-001, a selective PI3Kα inhibitor, for the treatment of slow-flow vascular malformations
一项针对低流速血管畸形的选择性PI3Kα抑制剂ART-001的II期随机、双盲试验
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-03564-z
Ozeki, Michio; Tanaka, Akira; Kuniyeda, Kanako; Nozaki, Taiki; Fujino, Akihiro; Nomura, Tadashi; Uemura, Naoto; Suenobu, Souichi; Aramaki-Hattori, Noriko; Hayashi, Ayato; Kato, Aiko; Kiyosue, Hiro; Imagawa, Kotaro; Nagao, Munetomo; Shimizu, Fumiaki; Ochi, Junko; Horiuchi, Saya; Ohyama, Tetsuji; Ando, Haruhi; Nagabukuro, Hiroshi