Cardiotropic AAV gene therapy for heart failure: a phase 1 trial
针对心力衰竭的心脏靶向性AAV基因疗法:一项I期试验
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-025-04011-z
Henry, Timothy D; Chung, Eugene S; Alvisi, Monica; Sethna, Ferzin; Murray, David R; Traverse, Jay H; Roessig, Lothar; Roberts, Luke; Reddy, Swarna; Chen, Youjun; Ozkan, Tugba Guven; Webb, Stacy; Mittal, Monika; Ervin, Leigh; Sadek, Hesham; Mikhail, Sheila; Haghighi, Kobra; Jiang, Canwen; Samulski, R Jude; Kranias, Evangelia G; Tretiakova, Anna P; Hajjar, Roger J