Treating neutropenia and neutrophil dysfunction in glycogen storage disease type Ib with an SGLT2 inhibitor
使用SGLT2抑制剂治疗Ib型糖原贮积症中的中性粒细胞减少症和中性粒细胞功能障碍
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2019004465
Wortmann, Saskia B; Van Hove, Johan L K; Derks, Terry G J; Chevalier, Nathalie; Knight, Vijaya; Koller, Andreas; Oussoren, Esmee; Mayr, Johannes A; van Spronsen, Francjan J; Lagler, Florian B; Gaughan, Sommer; Van Schaftingen, Emile; Veiga-da-Cunha, Maria