The Scope for Thalassemia Gene Therapy by Disruption of Aberrant Regulatory Elements
通过破坏异常调控元件进行地中海贫血基因治疗的范围
期刊:Journal of Clinical Medicine
影响因子:3
doi:10.3390/jcm8111959
Petros Patsali, Claudio Mussolino, Petros Ladas, Argyro Floga, Annita Kolnagou, Soteroula Christou, Maria Sitarou, Michael N Antoniou, Toni Cathomen, Carsten Werner Lederer, Marina Kleanthous