日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Association between treatment-emergent cytopenias and clinical responses to imetelstat in lower-risk myelodysplastic syndromes

低危骨髓增生异常综合征患者治疗期间出现的血细胞减少症与伊美替司他临床疗效之间的关联

Zeidan, Amer M; Santini, Valeria; Díez-Campelo, María; Savona, Michael R; Sekeres, Mikkael A; Madanat, Yazan F; Fenaux, Pierre; Raza, Azra; Mittelman, Moshe; Thépot, Sylvain; Buckstein, Rena; Germing, Ulrich; Valcárcel, David; Jonášová, Anna; Shah, Sheetal; Xia, Qi; Sun, Libo; Navada, Shyamala; Berry, Tymara; Platzbecker, Uwe; Komrokji, Rami S

Prognostic Model Combining Mutational and Cytogenetic Profiles in Acute Myeloid Leukemia Treated with Venetoclax and Hypomethylating Agents

结合突变和细胞遗传学特征的急性髓系白血病预后模型(采用维奈托克和去甲基化药物治疗)

Drekolias, Dimitrios; Tuz Zahra, Fatima; Fileni, Caroline; Sallman, David A; Mo, Qianxing; Chan, Onyee; Zhang, Ling; Vincelette, Nicole D; Yu, Xiaoqing; Sammut, Rinzine; Moon, Jungwon; Park, Junyoung; Umasangtongkul, Sura-Attha; Lledo, Felyschia M; Razabdouski, Tiffany N; Cheng, Chia-Ho; Qin, Dahui; Mai, Kathy; Ball, Somedeb; Shallis, Rory M; Xie, Zhuoer; Kuykendall, Andrew T; Padron, Eric; Sweet, Kendra; Walker, Alison R; Komrokji, Rami S; Lancet, Jeffrey E; Niyongere, Sandrine; Cluzeau, Thomas; Yun, Seongseok

Posttransplant MRD monitoring by TP53 duplex sequencing with APR-246 + azacitidine maintenance predicts outcomes

移植后采用TP53双链测序进行微小残留病(MRD)监测,并结合APR-246+阿扎胞苷维持治疗,可预测预后。

Sallman, David A; McLemore, Amy F; Komrokji, Rami; Elmariah, Hany; Kuykendall, Andrew T; Bejanyan, Nelli; Chan, Onyee; Faramand, Rawan; Pidala, Joseph; Yoder, Sean J; Perez, Lia; Nishihori, Taiga; Padron, Eric; Fernandez, Hugo; Lancet, Jeffrey E; Mishra, Asmita

Characterization and Clinical Implications of p53 Dysfunction in Patients With Myelodysplastic Syndromes

骨髓增生异常综合征患者p53功能障碍的特征及临床意义

Zampini, Matteo; Riva, Elena; Lanino, Luca; Sauta, Elisabetta; Antunes Dos Reis, Rita; Ejarque, Rosa Maria Andres; Maggioni, Giulia; Termanini, Alberto; Merlotti, Alessandra; Campagna, Alessia; Dall'Olio, Lorenzo; Kulasekararaj, Austin; Calvi, Michela; Di Vito, Clara; Bonometti, Arturo; Rahal, Daoud; Croci, Giorgio; Boveri, Emanuela; Gianelli, Umberto; Ponzoni, Maurilio; Caselli, Rossella; Albertazzi, Serena; Todisco, Gabriele; Ubezio, Marta; Crisafulli, Laura; Frigo, Alessandro; Lugli, Enrico; Mosca, Ettore; Acha, Pamela; Ghisletti, Serena; Nicassio, Francesco; Santoro, Armando; Diez-Campelo, Maria; Solé, Francesc; Ades, Lionel; Platzbecker, Uwe; Santini, Valeria; Fenaux, Pierre; Haferlach, Torsten; Sallman, David; Garcia-Manero, Guillermo; Mavilio, Domenico; Remondini, Daniel; Castellani, Gastone; D'Amico, Saverio; Zeidan, Amer M; Komrokji, Rami; Kordasti, Shahram; Ficara, Francesca; Della Porta, Matteo Giovanni

Reducing clinical trial eligibility barriers for patients with MDS: an icMDS position statement

降低MDS患者参与临床试验的门槛:icMDS立场声明

Borate, Uma; Pugh, Kelly; Waller, Allyson; Welkie, Rina Li; Huang, Ying; Bewersdorf, Jan Philipp; Stahl, Maximilian; DeZern, Amy E; Platzbecker, Uwe; Sekeres, Mikkael A; Wei, Andrew H; Buckstein, Rena J; Roboz, Gail J; Savona, Michael R; Loghavi, Sanam; Hasserjian, Robert P; Fenaux, Pierre; Sallman, David A; Hourigan, Christopher S; Della Porta, Matteo Giovanni; Nimer, Stephen; Little, Richard F; Santini, Valeria; Efficace, Fabio; Taylor, Justin; Garcia-Manero, Guillermo; Odenike, Olatoyosi; Kim, Tae Kon; Halene, Stephanie; Komrokji, Rami S; Griffiths, Elizabeth A; Greenberg, Peter L; Xu, Mina L; Xie, Zhuoer; Bejar, Rafael; Sanz, Guillermo F; Patnaik, Mrinal M; Figueroa, Maria; Carraway, Hetty E; Abdel-Wahab, Omar; Starczynowski, Daniel; Padron, Eric; Boultwood, Jacqueline; Gore, Steven; Daver, Naval G; Churpek, Jane E; Majeti, Ravindra; Bennett, John M; List, Alan F; Brunner, Andrew M; Zeidan, Amer M

Long-term follow-up and combined Phase 2 results of eprenetapopt and azacitidine in patients with TP53 mutant MDS/AML

长期随访及eprenetapopt联合阿扎胞苷治疗TP53突变型MDS/AML患者的II期联合试验结果

Sallman, David A; Komrokji, Rami S; Dezern, Amy E; Sebert, Marie; Garcia-Manero, Guillermo; Rahmé, Ramy; Winer, Eric S; Lehmann-Che, Jacqueline; Roboz, Gail J; Madelaine, Isabelle; Sekeres, Mikkael A; Peterlin, Pierre; Chan, Onyee; Beyne-Rauzy, Odile; Kuykendall, Andrew; Recher, Christian; McLemore, Amy; Stamatoullas, Aspasia; Zhang, Ling; Willems, Lise; Mo, Qianxing; Raffoux, Emmanuel; Nardelli, Lisa; Berthon, Céline; Al Ali, Najla H; Quesnel, Bruno; Padron, Eric; Kantarjian, Hagop M; List, Alan F; Ades, Lionel; Lancet, Jeffrey E; Fenaux, Pierre; Cluzeau, Thomas

Response to luspatercept can be predicted and improves overall survival in the real-life treatment of LR-MDS

在真实世界中,对鲁帕西普的反应可以预测,并且能够改善低危骨髓增生异常综合征(LR-MDS)患者的总体生存期。

Consagra, Angela; Lanino, Luca; Al Ali, Najla H; Aguirre, Luis; Xie, Zhuoer; Chan, Onyee; Andreossi, Gloria; Raddi, Marco G; Rigodanza, Luca; Sanna, Alessandro; Mattiuz, Giorgio; Tofacchi, Elena; Amato, Cristina; Tanturli, Michele; De Pourcq, Sven; Walker, Alison; Kuykendall, Andrew; Lancet, Jeffrey; Padron, Eric; Sallman, David A; Restuccia, Francesco; Perego, Alessandra; Ubezio, Marta; Fattizzo, Bruno; Riva, Marta; Maggioni, Giulia; Campagna, Alessia; Della Porta, Matteo G; Santini, Valeria; Komrokji, Rami S

Haploinsufficiency of miR-143 and miR-145 reveal targetable dependencies in resistant del(5q) myelodysplastic neoplasm.

miR-143 和 miR-145 的单倍体不足揭示了耐药性 del(5q) 骨髓增生异常综合征中可靶向的依赖性

Gharaee Nadia, Wegrzyn-Woltosz Joanna, Jiang Jihong, Akhade Vijay Suresh, Bridgers Joshua, Stubbins Ryan J, Hiwase Devendra, Kutyna Monika M, Chan Onyee, Komrokji Rami, Padron Eric, Deng Yu, Cole Gary, Umlandt Patricia, Fuller Megan, Kim Ada, Karsan Aly

Effect of prior therapy on the clinical activity of imetelstat in patients with transfusion-dependent, ESA-relapsed or -refractory/-ineligible LR-MDS

既往治疗对输血依赖型、ESA复发或难治/不适合接受ESA治疗的低危骨髓增生异常综合征(LR-MDS)患者使用伊美替司他(imetelstat)临床疗效的影响

Komrokji, Rami S; Santini, Valeria; Zeidan, Amer M; Sekeres, Mikkael A; Fenaux, Pierre; Raza, Azra; Mittelman, Moshe; Thépot, Sylvain; Buckstein, Rena; Germing, Ulrich; Madanat, Yazan F; Díez-Campelo, María; Valcárcel, David; Jonášová, Anna; Dougherty, Souria; Shah, Sheetal; Xia, Qi; Sun, Libo; Navada, Shyamala; Feller, Faye; Savona, Michael R; Platzbecker, Uwe

Genetic predisposition to persistent fatigue after a diagnosis of colorectal cancer

遗传因素导致结直肠癌确诊后持续疲劳

Kazemian, Elham; Mo, Qianxing; Matejcic, Marco; Tsai, Ya-Yu; Sobieski, Daniel; Li, Xiaoyin; Hoogland, Aasha I; Crowder, Sylvia L; Gonzalez, Brian D; Oswald, Laura B; Sleight, Alix G; Nguyen, Nathalie; Loroña, Nicole C; Damerell, Victoria; Komrokji, Khaled R; Mooney, Kathi; Playdon, Mary C; Ulrich, Cornelia M; Li, Christopher I; Shibata, David; Toriola, Adetunji T; Ose, Jennifer; Peoples, Anita R; Hardikar, Sheetal; Kahlert, Christoph; Siegel, Erin M; Bower, Julienne E; Schmit, Stephanie L; Gigic, Biljana; Jim, Heather S L; Figueiredo, Jane C