日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Functional correction and genome integrity with duplex base editing of β-thalassemic hematopoietic stem cells

利用β-地中海贫血造血干细胞的双链碱基编辑实现功能矫正和基因组完整性

Papaioannou, Nikoletta Y; Patsali, Petros; Klermund, Julia; Papasavva, Panayiota L; Andrieux, Geoffroy; Koniali, Lola; Naiisseh, Basma; Christou, Soteroula; Sitarou, Maria; Kleanthous, Marina; Cathomen, Toni; Lederer, Carsten W

Fluoride Release, Recharge, and Mass Stability of Restorative Dental Materials: An In Vitro Study

牙科修复材料的氟释放、再充填和质量稳定性:一项体外研究

Islam, Md Sofiqul; Padmanabhan, Vivek; Koniali, Ghaid; Alabdin, Mohannad Zain; Aryal Ac, Smriti; Hashim, Nada Tawfig; Elsayed, Mohamed Ahmed; Rahman, Muhammed Mustahsen

Efficacy and Safety of Concomitant Surgical Ablation During Mitral Valve Replacement: A Systematic Review

二尖瓣置换术中同期外科消融术的疗效和安全性:系统评价

Hamodat, Omar; Almuzainy, Saif; Yahya, Rand; Alzaatreh, Razan; Haroon, Samiullah; Koniali, Salam

An Updated Meta-Analysis of Patent Foramen Ovale Closure Versus Medical Therapy for Preventing Recurrent Cryptogenic Stroke

卵圆孔未闭封堵术与药物治疗预防复发性隐源性卒中的最新荟萃分析

Almuzainy, Saif; Hamodat, Omar; Yahya, Rand; Koniali, Salam; Qaisar, Rizwan

Context base editing for splice correction of IVSI-110 β-thalassemia

用于 IVSI-110 β-地中海贫血剪接校正的上下文库编辑

Basma Naiisseh, Panayiota L Papasavva, Nikoletta Y Papaioannou, Marios Tomazou, Lola Koniali, Xenia Felekis, Constantina G Constantinou, Maria Sitarou, Soteroula Christou, Marina Kleanthous, Carsten W Lederer, Petros Patsali

Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBBAS3 Gene Addition and Mutation-Specific RNA Interference

通过 HBBAS3 基因添加和突变特异性 RNA 干扰对 β-地中海贫血进行治疗的单体和双功能 GLOBE 载体的评估

Lola Koniali, Christina Flouri, Markela I Kostopoulou, Nikoletta Y Papaioannou, Panayiota L Papasavva, Basma Naiisseh, Coralea Stephanou, Anthi Demetriadou, Maria Sitarou, Soteroula Christou, Michael N Antoniou, Marina Kleanthous, Petros Patsali, Carsten W Lederer

High-efficiency editing in hematopoietic stem cells and the HUDEP-2 cell line based on in vitro mRNA synthesis

基于体外 mRNA 合成的造血干细胞和 HUDEP-2 细胞系高效编辑

Nikoletta Y Papaioannou, Petros Patsali, Basma Naiisseh, Panayiota L Papasavva, Lola Koniali, Ryo Kurita, Yukio Nakamura, Soteroula Christou, Maria Sitarou, Claudio Mussolino, Toni Cathomen, Marina Kleanthous, Carsten W Lederer

Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies

及早发现:产前和儿童期应用先进疗法的框架参数和进展

Lederer, Carsten W; Koniali, Lola; Buerki-Thurnherr, Tina; Papasavva, Panayiota L; La Grutta, Stefania; Licari, Amelia; Staud, Frantisek; Bonifazi, Donato; Kleanthous, Marina

Repression of sphingosine kinase (SK)-interacting protein (SKIP) in acute myeloid leukemia diminishes SK activity and its re-expression restores SK function

急性髓系白血病中鞘氨醇激酶(SK)相互作用蛋白(SKIP)的抑制会降低SK活性,而其重新表达则可恢复SK功能。

Ghazaly, Essam A; Miraki-Moud, Farideh; Smith, Paul; Gnanaranjan, Chathunissa; Koniali, Lola; Oke, Adedayo; Saied, Marwa H; Petty, Robert; Matthews, Janet; Stronge, Randal; Joel, Simon P; Young, Bryan D; Gribben, John; Taussig, David C

Alport syndrome: Proteomic analysis identifies early molecular pathway alterations in Col4a3 knock out mice

阿尔波特综合征:蛋白质组学分析确定 Col4a3 基因敲除小鼠的早期分子通路改变

Orthodoxia Nicolaou, Andreas Kousios, Kleitos Sokratous, Louiza Potamiti, Lola Koniali, George Neophytou, Revekka Papacharalampous, Maria Zanti, Kyriakos Ioannou, Andreas Hadjisavvas, Christoph Stingl, Theo M Luider, Kyriacos Kyriacou